Department of Neurosurgery, Yale School of Medicine, New Haven, Connecticut, USA.
Nat Genet. 2011 Jun;43(6):590-4. doi: 10.1038/ng.836. Epub 2011 May 15.
The biological basis for regional and inter-species differences in cerebral cortical morphology is poorly understood. We focused on consanguineous Turkish families with a single affected member with complex bilateral occipital cortical gyration abnormalities. By using whole-exome sequencing, we initially identified a homozygous 2-bp deletion in LAMC3, the laminin γ3 gene, leading to an immediate premature termination codon. In two other affected individuals with nearly identical phenotypes, we identified a homozygous nonsense mutation and a compound heterozygous mutation. In human but not mouse fetal brain, LAMC3 is enriched in postmitotic cortical plate neurons, localizing primarily to the somatodendritic compartment. LAMC3 expression peaks between late gestation and late infancy, paralleling the expression of molecules that are important in dendritogenesis and synapse formation. The discovery of the molecular basis of this unusual occipital malformation furthers our understanding of the complex biology underlying the formation of cortical gyrations.
大脑皮质形态在区域和种间存在差异的生物学基础尚未被充分理解。我们专注于具有单一受累成员的近亲土耳其家族,这些成员患有复杂的双侧枕叶皮质回旋异常。通过使用全外显子组测序,我们最初鉴定出 LAMC3(层粘连蛋白 γ3 基因)中的纯合 2 个碱基缺失,导致立即出现过早终止密码子。在另外两个具有几乎相同表型的受累个体中,我们鉴定出纯合无义突变和复合杂合突变。在人类而非小鼠胎儿脑中,LAMC3 在有丝后皮质板神经元中富集,主要定位于体树突质区。LAMC3 的表达在妊娠后期和婴儿后期达到峰值,与在树突发生和突触形成中起重要作用的分子的表达相平行。发现这种不寻常的枕部畸形的分子基础,进一步加深了我们对皮质回旋形成所涉及的复杂生物学的理解。