Department of Biostatistics, School of Medicine, Vanderbilt University, Nashville, TN, USA.
J Pharmacokinet Pharmacodyn. 2011 Oct;38(5):613-36. doi: 10.1007/s10928-011-9211-7. Epub 2011 Aug 17.
The purpose of this study is to develop a statistical methodology to handle a large proportion of artifactual outliers in a population pharmacokinetic (PK) modeling. The motivating PK data were obtained from a population PK study to examine associations between PK parameters such as clearance of dexmedetomidine (DEX) and cytochrome P450 2A6 phenotypes. The blood samples were sparsely sampled from patients in intensive care units (ICUs) while different doses of DEX were continuously infused. Conventional population PK analysis of these data revealed several challenges and intricacies. Especially, there was strong evidence that some plasma drug concentrations were artifactually high and likely contaminated with the infused drug due to blood sampling processes that are sometimes unavoidable in an ICU setting. If not addressed, or if arbitrarily excluded, these outlying values could lead to biased estimates of PK parameters and miss important relationships between PK parameters and covariates due to increased variability. We propose a novel population PK model, a Bayesian hierarchical nonlinear mixture model, to accommodate the artifactual outliers using a finite mixture as the residual error model. Our results showed that the proposed model handles the outliers well. We also conducted simulation studies with a varying proportion of the outliers. These simulation results showed that the proposed model can accommodate the outliers well so that the estimated PK parameters are less biased.
本研究旨在开发一种统计方法,以处理群体药代动力学(PK)建模中大量人为异常值。本研究的 PK 数据来源于一项 PK 研究,旨在探讨去甲肾上腺素(DEX)清除率等 PK 参数与细胞色素 P450 2A6 表型之间的关系。这些血液样本是从重症监护病房(ICU)的患者中稀疏采集的,同时持续输注不同剂量的 DEX。对这些数据进行常规的群体 PK 分析揭示了一些挑战和复杂性。特别是,有强烈的证据表明,由于 ICU 环境中有时不可避免的采血过程,一些血浆药物浓度人为地过高,并且可能受到输注药物的污染。如果不加以处理,或者任意排除这些异常值,这些异常值可能会导致 PK 参数的估计值出现偏差,并由于变异性增加而错过 PK 参数与协变量之间的重要关系。我们提出了一种新的群体 PK 模型,即贝叶斯层次非线性混合模型,通过使用有限混合作为残差误差模型来适应人为异常值。研究结果表明,所提出的模型能够很好地处理异常值。我们还进行了具有不同比例异常值的模拟研究。这些模拟结果表明,所提出的模型能够很好地适应异常值,从而使估计的 PK 参数的偏差更小。