Clinical and Molecular Genetics and Neurosciences Units, University College London Institute of Child Health, London and Metabolic and Neurosciences Units, Great Ormond Street Hospital for Children NHS Trust, London, UK.
Dev Med Child Neurol. 2013 Jan;55(1):23-36. doi: 10.1111/j.1469-8749.2012.04406.x. Epub 2012 Sep 24.
Seizures may be the first and the major presenting feature of an inborn error of metabolism (IEM), for example in a neonate with pyridoxine-dependent epilepsy. In other IEMs, seizures may be preceded by other major symptoms: by a reduced level of consciousness in a child with an organic acidaemia or urea cycle defect; or by loss of skills, progressive weakness, ataxia, and upper motor signs in a child with a lysosomal storage disorder or peroxisomal leukodystrophy. This review concentrates on those IEMs for which specific treatment is available. The common metabolic causes of seizures vary according to the age at presentation. Features from the history, examination, imaging, and first line biochemical investigations can all provide clues to an inborn error. This review attempts to delineate these and to provide a guide to the specific tests that can be used to make the diagnosis of disorders with specific treatment.
癫痫发作可能是先天性代谢缺陷(IEM)的首发和主要表现特征,例如依赖吡哆醇的癫痫新生儿。在其他 IEM 中,癫痫发作可能先于其他主要症状:有机酸血症或尿素循环缺陷患儿可能表现为意识水平降低;溶酶体贮积症或过氧化物酶体脑白质营养不良患儿可能表现为技能丧失、进行性无力、共济失调和上运动体征。本综述重点关注那些有特定治疗方法的 IEM。根据发病年龄,癫痫发作的常见代谢原因有所不同。病史、检查、影像学和一线生化检查的特征都可以为先天性错误提供线索。本综述试图描述这些特征,并提供一个指南,以指导使用特定的测试来诊断具有特定治疗方法的疾病。