Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts, USA.
Nat Genet. 2013 Mar;45(3):285-9. doi: 10.1038/ng.2526. Epub 2013 Jan 20.
Meningiomas are the most common primary nervous system tumor. The tumor suppressor NF2 is disrupted in approximately half of all meningiomas, but the complete spectrum of genetic changes remains undefined. We performed whole-genome or whole-exome sequencing on 17 meningiomas and focused sequencing on an additional 48 tumors to identify and validate somatic genetic alterations. Most meningiomas had simple genomes, with fewer mutations, rearrangements and copy-number alterations than reported in other tumors in adults. However, several meningiomas harbored more complex patterns of copy-number changes and rearrangements, including one tumor with chromothripsis. We confirmed focal NF2 inactivation in 43% of tumors and found alterations in epigenetic modifiers in an additional 8% of tumors. A subset of meningiomas lacking NF2 alterations harbored recurrent oncogenic mutations in AKT1 (p.Glu17Lys) and SMO (p.Trp535Leu) and exhibited immunohistochemical evidence of activation of these pathways. These mutations were present in therapeutically challenging tumors of the skull base and higher grade. These results begin to define the spectrum of genetic alterations in meningiomas and identify potential therapeutic targets.
脑膜瘤是最常见的原发性神经系统肿瘤。肿瘤抑制因子 NF2 在大约一半的脑膜瘤中被破坏,但完整的遗传改变谱仍未定义。我们对 17 例脑膜瘤进行了全基因组或全外显子组测序,并对另外 48 例肿瘤进行了重点测序,以鉴定和验证体细胞遗传改变。大多数脑膜瘤具有简单的基因组,与成人其他肿瘤相比,其突变、重排和拷贝数改变较少。然而,一些脑膜瘤具有更复杂的拷贝数变化和重排模式,包括一个具有染色体碎裂的肿瘤。我们在 43%的肿瘤中证实了 NF2 的局部失活,并在另外 8%的肿瘤中发现了表观遗传修饰因子的改变。一部分缺乏 NF2 改变的脑膜瘤中存在 AKT1(p.Glu17Lys)和 SMO(p.Trp535Leu)的复发性致癌突变,并表现出这些途径激活的免疫组织化学证据。这些突变存在于具有治疗挑战性的颅底和高级别肿瘤中。这些结果开始定义脑膜瘤的遗传改变谱,并确定潜在的治疗靶点。