Preiksaitiene Egle, Molytė Alma, Kasnauskiene Jurate, Ciuladaite Zivile, Utkus Algirdas, Patsalis Philippos C, Kučinskas Vaidutis
Department of Human and Medical Genetics, Faculty of Medicine, Vilnius University, Santariškių st. 2, 08661, Vilnius, Lithuania,
J Appl Genet. 2014 May;55(2):189-96. doi: 10.1007/s13353-014-0197-x. Epub 2014 Feb 18.
Since the introduction of high-resolution microarray technologies, it has become apparent that structural chromosomal rearrangements can lead to a wide variety of clinical manifestations, including developmental delay/intellectual disability (DD/ID). It has been shown previously that the diagnostic yield of genome-wide array-based identification of submicroscopic alterations in patients with ID varies widely and depends on the patient selection criteria. More attempts have recently been made to define the phenotypic clues of pathogenic copy number variants (CNVs). The aim of this study was to investigate a well-phenotyped cohort of patients with DD/ID and determine whether certain clinical features may serve as indicators for pathogenic CNVs. A retrospective analysis was conducted for patients with DD/ID (n = 211) who were tested using genome-wide chromosomal microarray technologies and a review of the clinical data was performed. Pathogenic CNVs were detected in 29 patients. In comparison with individuals who had normal molecular karyotyping results (n = 182), malformations of the musculoskeletal system; congenital malformations of the CNS (particularly hydrocephalus and congenital malformations of the corpus callosum); minor anomalies of the eye, face, and neck subgroup (particularly downward-slanting palpebral fissures, minor anomalies of the ear, and micrognathia); brachydactyly; and umbilical hernia were more common in patients with chromosomal alterations. A multivariate logistic regression analysis allowed the identification of three independent pathogenic CNV predictors: congenital malformations of the corpus callosum, minor anomalies of the ear, and brachydactyly. Insights into the chromosomal phenotype may help to increase the diagnostic yield of microarray technologies and sharpen the distinction between chromosomal alterations and other conditions.
自从高分辨率微阵列技术问世以来,结构染色体重排会导致包括发育迟缓/智力残疾(DD/ID)在内的多种临床表现这一点已变得十分明显。此前已有研究表明,基于全基因组阵列识别智障患者亚微观改变的诊断率差异很大,且取决于患者选择标准。最近人们进行了更多尝试来确定致病性拷贝数变异(CNV)的表型线索。本研究的目的是调查一组具有明确表型的DD/ID患者,并确定某些临床特征是否可作为致病性CNV的指标。对使用全基因组染色体微阵列技术进行检测的DD/ID患者(n = 211)进行了回顾性分析,并对临床数据进行了审查。在29例患者中检测到致病性CNV。与分子核型分析结果正常的个体(n = 182)相比,染色体改变的患者中骨骼肌肉系统畸形;中枢神经系统先天性畸形(尤其是脑积水和胼胝体先天性畸形);眼、面部和颈部亚组的轻微异常(尤其是睑裂向下倾斜、耳部轻微异常和小颌畸形);短指畸形;以及脐疝更为常见。多因素逻辑回归分析确定了三个独立的致病性CNV预测指标:胼胝体先天性畸形、耳部轻微异常和短指畸形。对染色体表型的深入了解可能有助于提高微阵列技术的诊断率,并更清晰地区分染色体改变与其他病症。