Thompson Rachel, Johnston Louise, Taruscio Domenica, Monaco Lucia, Béroud Christophe, Gut Ivo G, Hansson Mats G, 't Hoen Peter-Bram A, Patrinos George P, Dawkins Hugh, Ensini Monica, Zatloukal Kurt, Koubi David, Heslop Emma, Paschall Justin E, Posada Manuel, Robinson Peter N, Bushby Kate, Lochmüller Hanns
Institute of Genetic Medicine, MRC Centre for Neuromuscular Diseases, Newcastle University, London, UK.
J Gen Intern Med. 2014 Aug;29 Suppl 3(Suppl 3):S780-7. doi: 10.1007/s11606-014-2908-8.
Research into rare diseases is typically fragmented by data type and disease. Individual efforts often have poor interoperability and do not systematically connect data across clinical phenotype, genomic data, biomaterial availability, and research/trial data sets. Such data must be linked at both an individual-patient and whole-cohort level to enable researchers to gain a complete view of their disease and patient population of interest. Data access and authorization procedures are required to allow researchers in multiple institutions to securely compare results and gain new insights. Funded by the European Union's Seventh Framework Programme under the International Rare Diseases Research Consortium (IRDiRC), RD-Connect is a global infrastructure project initiated in November 2012 that links genomic data with registries, biobanks, and clinical bioinformatics tools to produce a central research resource for rare diseases.
罕见病研究通常因数据类型和疾病而碎片化。个体研究往往互操作性较差,无法系统地将临床表型、基因组数据、生物材料可用性以及研究/试验数据集的数据联系起来。此类数据必须在个体患者和整个队列层面进行关联,以便研究人员全面了解他们所关注的疾病和患者群体。需要数据访问和授权程序,使多个机构的研究人员能够安全地比较结果并获得新见解。由国际罕见病研究联盟(IRDiRC)在欧盟第七框架计划资助下,RD-Connect是一个于2012年11月启动的全球基础设施项目,它将基因组数据与登记处、生物样本库和临床生物信息学工具相连接,以生成一个罕见病中央研究资源。