Klar Joakim, Hisatsune Chihiro, Baig Shahid M, Tariq Muhammad, Johansson Anna C V, Rasool Mahmood, Malik Naveed Altaf, Ameur Adam, Sugiura Kotomi, Feuk Lars, Mikoshiba Katsuhiko, Dahl Niklas
J Clin Invest. 2014 Nov;124(11):4773-80. doi: 10.1172/JCI70720. Epub 2014 Oct 20.
There are 3 major sweat-producing glands present in skin; eccrine, apocrine, and apoeccrine glands. Due to the high rate of secretion, eccrine sweating is a vital regulator of body temperature in response to thermal stress in humans; therefore, an inability to sweat (anhidrosis) results in heat intolerance that may cause impaired consciousness and death. Here, we have reported 5 members of a consanguineous family with generalized, isolated anhidrosis, but morphologically normal eccrine sweat glands. Whole-genome analysis identified the presence of a homozygous missense mutation in ITPR2, which encodes the type 2 inositol 1,4,5-trisphosphate receptor (InsP3R2), that was present in all affected family members. We determined that the mutation is localized within the pore forming region of InsP3R2 and abrogates Ca2+ release from the endoplasmic reticulum, which suggests that intracellular Ca2+ release by InsP3R2 in clear cells of the sweat glands is important for eccrine sweat production. Itpr2-/- mice exhibited a marked reduction in sweat secretion, and evaluation of sweat glands from Itpr2-/- animals revealed a decrease in Ca2+ response compared with controls. Together, our data indicate that loss of InsP3R2-mediated Ca2+ release causes isolated anhidrosis in humans and suggest that specific InsP3R inhibitors have the potential to reduce sweat production in hyperhidrosis.
皮肤中有3种主要的汗腺:小汗腺、顶泌汗腺和顶浆分泌小汗腺。由于分泌速率高,在人类中,小汗腺出汗是响应热应激调节体温的重要机制;因此,无法出汗(无汗症)会导致耐热性下降,可能会引起意识障碍甚至死亡。在此,我们报告了一个近亲结婚家庭中的5名成员,他们患有全身性、孤立性无汗症,但小汗腺形态正常。全基因组分析确定,在所有患病家庭成员中,编码2型肌醇1,4,5-三磷酸受体(InsP3R2)的ITPR2存在纯合错义突变。我们确定该突变位于InsP3R2的孔形成区域内,可消除内质网释放Ca2+,这表明汗腺透明细胞中InsP3R2介导的细胞内Ca2+释放对于小汗腺排汗很重要。Itpr2-/-小鼠的汗液分泌明显减少,对Itpr2-/-动物的汗腺评估显示,与对照组相比,Ca2+反应降低。我们的数据共同表明,InsP3R2介导的Ca2+释放缺失会导致人类出现孤立性无汗症,并表明特定的InsP3R抑制剂有可能减少多汗症患者的汗液分泌。