Smith Angela R, Warlick Erica D, Roesler Michelle A, Poynter Jenny N, Richardson Michaela, Nguyen Phuong, Cioc Adina, Hirsch Betsy, Ross Julie A
Division of Blood and Marrow Transplantation, Department of Pediatrics, University of Minnesota, 420 Delaware Street SE; MMC 484, Minneapolis, MN, 55455, USA,
Ann Hematol. 2015 Oct;94(10):1667-75. doi: 10.1007/s00277-015-2422-z. Epub 2015 Jun 11.
Myelodysplastic syndrome (MDS) is a clonal hematopoietic stem cell disorder characterized by dysplastic changes in the bone marrow, ineffective erythropoiesis, and an increased risk of developing acute myeloid leukemia. Treatment planning for patients with MDS is a complex process, and we sought to better characterize hematopoietic cell transplantation (HCT) outcomes and the factors that play into decision-making regarding referral of adults with MDS for definitive therapy with HCT. Patients enrolled in a population-based study of MDS between April 2010 and January 2013 who underwent HCT within the first year after enrollment were included in this analysis. Age- and risk-matched MDS patient controls also enrolled during that time period were used as a comparison. Survival was significantly better in the HCT group (48 vs. 21 %, log-rank p value 0.009). Non-HCT patients were more likely to have comorbidities, and HCT patients were more likely to have a college degree and an income >$80,000. All three of these variables were independently associated with HCT, but none impacted survival. Patients with MDS in our study who underwent HCT had better survival than a comparable group of patients who did not undergo HCT. With refined treatment techniques, more patients may be able to be considered for this therapy. More work needs to be done to determine why education and income appear to impact the decision to pursue HCT, but these factors may impact referral to an academic center where aggressive therapy like HCT is more likely to be considered.
骨髓增生异常综合征(MDS)是一种克隆性造血干细胞疾病,其特征为骨髓发育异常改变、无效红细胞生成以及发生急性髓系白血病的风险增加。MDS患者的治疗规划是一个复杂的过程,我们试图更好地描述造血细胞移植(HCT)的结果以及影响将成年MDS患者转诊接受HCT确定性治疗决策的因素。纳入本分析的患者为2010年4月至2013年1月期间参与一项基于人群的MDS研究且在入组后第一年内接受HCT的患者。同时纳入在此期间入组的年龄和风险匹配的MDS患者作为对照。HCT组的生存率显著更高(48%对21%,对数秩检验p值为0.009)。非HCT患者更可能有合并症,而HCT患者更可能拥有大学学历且收入超过8万美元。所有这三个变量均与HCT独立相关,但均不影响生存率。我们研究中接受HCT的MDS患者比未接受HCT的可比患者组生存率更高。随着治疗技术的改进,可能有更多患者能够考虑接受这种治疗。需要开展更多工作来确定为何教育程度和收入似乎会影响接受HCT治疗的决策,但这些因素可能会影响转诊至更有可能考虑像HCT这样积极治疗的学术中心。