Mariño Laura, Pauwels Kris, Casasnovas Rodrigo, Sanchis Pilar, Vilanova Bartolomé, Muñoz Francisco, Donoso Josefa, Adrover Miquel
Institut Universitari d'Investigació en Ciències de la Salut (IUNICS). Departament de Química, Universitat de les Illes Balears, Ctra. Valldemossa km 7.5, E-07122 Palma de Mallorca, Spain.
1] Structural Biology Brussels, Vrije Universiteit Brussel, Pleinlaan 2, 1050 Brussel, Belgium [2] VIB Structural Biology Research Centre, Vlaams Instituut voor Biotechnologie, Pleinlaan 2, 1050 Brussel, Belgium.
Sci Rep. 2015 Jul 14;5:12052. doi: 10.1038/srep12052.
Protein aggregation with the concomitant formation of amyloid fibrils is related to several neurodegenerative diseases, but also to non-neuropathic amyloidogenic diseases and non-neurophatic systemic amyloidosis. Lysozyme is the protein involved in the latter, and it is widely used as a model system to study the mechanisms underlying fibril formation and its inhibition. Several phenolic compounds have been reported as inhibitors of fibril formation. However, the anti-aggregating capacity of other heteroaromatic compounds has not been studied in any depth. We have screened the capacity of eleven different hydroxypyridines to affect the acid-induced fibrillization of hen lysozyme. Although most of the tested hydroxypyridines alter the fibrillation kinetics of HEWL, only 3-hydroxy-2-methylpyridine, 3-hydroxy-6-methylpyridine and 3-hydroxy-2,6-dimethylpyridine completely abolish fibril formation. Different biophysical techniques and several theoretical approaches are combined to elucidate their mechanism of action. O-methylated 3-hydroxypyridines bind non-cooperatively to two distinct but amyloidogenic regions of monomeric lysozyme. This stabilises the protein structure, as evidenced by enhanced thermal stability, and results in the inhibition of the conformational transition that precedes fibril assembly. Our results point to o-methylated 3-hydroxypyridines as a promising molecular scaffold for the future development of novel fibrillization inhibitors.
蛋白质聚集并伴随淀粉样纤维的形成与多种神经退行性疾病相关,同时也与非神经性淀粉样变性疾病和非神经源性系统性淀粉样变性有关。溶菌酶是参与后者的蛋白质,它被广泛用作研究纤维形成及其抑制机制的模型系统。已有报道称几种酚类化合物可作为纤维形成的抑制剂。然而,其他杂环芳香族化合物的抗聚集能力尚未得到深入研究。我们筛选了十一种不同羟基吡啶影响酸诱导的鸡溶菌酶纤维化的能力。尽管大多数测试的羟基吡啶改变了蛋清溶菌酶的纤维化动力学,但只有3-羟基-2-甲基吡啶、3-羟基-6-甲基吡啶和3-羟基-2,6-二甲基吡啶完全抑制了纤维的形成。我们结合了不同的生物物理技术和几种理论方法来阐明它们的作用机制。O-甲基化的3-羟基吡啶以非协同方式结合到单体溶菌酶的两个不同但具有淀粉样形成能力的区域。这稳定了蛋白质结构,热稳定性增强证明了这一点,并导致抑制了纤维组装之前的构象转变。我们的结果表明,O-甲基化的3-羟基吡啶是未来开发新型纤维化抑制剂的有前景的分子支架。