地中海贫血患者标准监测指南：地中海贫血纵向队列报告
Guidelines for the Standard Monitoring of Patients With Thalassemia: Report of the Thalassemia Longitudinal Cohort.
作者信息
Tubman Venée N, Fung Ellen B, Vogiatzi Maria, Thompson Alexis A, Rogers Zora R, Neufeld Ellis J, Kwiatkowski Janet L
机构信息
*Boston Children's Hospital, Boston, MA †Children's Hospital & Research Center Oakland, Oakland, CA ‡Weill Medical College of Cornell, New York, NY §Children's Memorial Hospital, Chicago, IL ∥University of Texas Southwestern Medical Center, Dallas, TX ¶Children's Hospital of Philadelphia, Philadelphia, PA.
出版信息
J Pediatr Hematol Oncol. 2015 Apr;37(3):e162-9. doi: 10.1097/MPH.0000000000000307.
Abstract
Chronic transfusion therapy has played a central role in extending life expectancy for patients with hemoglobinopathies such as thalassemia. However, this life-saving therapy is associated with numerous complications that now comprise the bulk of management considerations for patients with thalassemia. This review reports on the experience of the Thalassemia Longitudinal Cohort and reviews available literature to establish guidelines for the management of patients with thalassemia.
摘要
长期输血治疗在延长地中海贫血等血红蛋白病患者的预期寿命方面发挥了核心作用。然而，这种挽救生命的治疗方法会引发众多并发症，而这些并发症如今已成为地中海贫血患者管理考量的主要内容。本综述报告了地中海贫血纵向队列的经验，并回顾了现有文献，以制定地中海贫血患者的管理指南。
相似文献
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Guidelines for the Standard Monitoring of Patients With Thalassemia: Report of the Thalassemia Longitudinal Cohort.
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