Domínguez-Bendala Juan, Lanzoni Giacomo, Klein Dagmar, Álvarez-Cubela Silvia, Pastori Ricardo L
Diabetes Research Institute, University of Miami Miller School of Medicine, Miami, FL, USA; Department of Surgery, University of Miami Miller School of Medicine, Miami, FL, USA; Department of Cell Biology and Anatomy, University of Miami Miller School of Medicine, Miami, FL, USA.
Diabetes Research Institute, University of Miami Miller School of Medicine, Miami, FL, USA.
Trends Endocrinol Metab. 2016 Mar;27(3):153-162. doi: 10.1016/j.tem.2015.12.003. Epub 2016 Jan 7.
Islet transplantation is an effective cell therapy for type 1 diabetes (T1D) but its clinical application is limited due to shortage of donors. After a decade-long period of exploration of potential alternative cell sources, the field has only recently zeroed in on two of them as the most likely to replace islets. These are pluripotent stem cells (PSCs) (through directed differentiation) and pancreatic non-endocrine cells (through directed differentiation or reprogramming). Here we review progress in both areas, including the initiation of Phase I/II clinical trials using human embryonic stem cell (hESc)-derived progenitors, advances in hESc differentiation in vitro, novel insights on the developmental plasticity of the pancreas, and groundbreaking new approaches to induce β cell conversion from the non-endocrine compartment without genetic manipulation.
胰岛移植是治疗1型糖尿病(T1D)的一种有效细胞疗法,但由于供体短缺,其临床应用受到限制。经过长达十年对潜在替代细胞来源的探索,该领域直到最近才将目光聚焦在其中两种最有可能替代胰岛的细胞来源上。这两种细胞来源是多能干细胞(PSC)(通过定向分化)和胰腺非内分泌细胞(通过定向分化或重编程)。在此,我们综述这两个领域的进展,包括使用人胚胎干细胞(hESc)衍生祖细胞开展的I/II期临床试验的启动、hESc体外分化的进展、对胰腺发育可塑性的新见解,以及在不进行基因操作的情况下诱导非内分泌细胞向β细胞转化的开创性新方法。