From the Institute for Neurodegenerative Disorders and Molecular NeuroImaging, New Haven, CT.
Neurology. 2016 Feb 23;86(8):748-54. doi: 10.1212/WNL.0000000000002391. Epub 2016 Jan 22.
To evaluate whether striatal [(18)F]MNI-659 PET imaging of phosphodiesterase 10A (PDE10) serves as a sensitive and reliable biomarker of striatal neurodegeneration in a longitudinal cohort of participants with early Huntington disease (HD).
A cohort of participants with HD, including both participants premanifest or manifest with motor signs, underwent clinical assessments, genetic determination, and 2 [(18)F]MNI-659 PET imaging sessions approximately 1 year apart. Eleven healthy control (HC) participants underwent clinical assessments and [(18)F]MNI-659 PET imaging once. Striatal binding potentials (BPnd) were estimated for brain regions of interest, specifically within the basal ganglia, and compared between baseline and follow-up imaging. Clinical measures of HD severity were assessed at each visit.
Eight participants with HD (6 manifest; 2 premanifest) participated. Of those with manifest HD, all had relatively early stage disease (stage 1, n = 2; stage 2, n = 4) and a Unified Huntington's Disease Rating Scale total motor score <45. As expected, the HD cohort as a whole had a reduction in the basal ganglia BPnd to approximately 50% of that seen in HC. On follow-up scans, [(18)F]MNI-659 uptake declined in the putamen and caudate nucleus in all 8 participants. The mean annualized rates of decline in signal in the caudate, putamen, and globus pallidus and the putamen were 16.6%, 6.9%, and 5.8%, respectively. In HC, the annualized reduction in signal in striatal regions was less than 1%.
Longitudinal data in this small cohort of participants with early HD support [(18)F]MNI-659 PET imaging of PDE10 as a useful biomarker to track HD disease progression.
评估磷酸二酯酶 10A(PDE10)的纹状体 [(18)F]MNI-659 PET 成像是否可作为早期亨廷顿病(HD)患者纵向队列中纹状体神经退行性变的敏感和可靠生物标志物。
一项包括运动症状前或表现型的 HD 参与者的队列接受了临床评估、基因确定以及大约相隔 1 年的 2 次 [(18)F]MNI-659 PET 成像检查。11 名健康对照(HC)参与者仅接受了临床评估和 [(18)F]MNI-659 PET 成像检查。在基线和随访成像时,估计了脑区(特别是基底神经节)的纹状体结合潜能(BPnd),并对其进行了比较。每次就诊时都评估了 HD 严重程度的临床指标。
8 名 HD 参与者(6 名表现型;2 名症状前)参与了研究。表现型 HD 患者均处于疾病早期阶段(1 期,n = 2;2 期,n = 4),且统一亨廷顿病评定量表的总运动评分<45。正如预期的那样,整个 HD 队列的基底神经节 BPnd 降低至 HC 的约 50%。在随访扫描中,8 名参与者的纹状体中的 [(18)F]MNI-659 摄取均减少。纹状体、尾状核和苍白球的信号平均每年下降率分别为 16.6%、6.9%和 5.8%,而纹状体的下降率为 6.9%。在 HC 中,纹状体区域的信号每年下降率小于 1%。
这项早期 HD 小队列的纵向数据支持 [(18)F]MNI-659 PET 成像 PDE10 作为一种有用的生物标志物,用于跟踪 HD 疾病进展。