Kotarek Joseph, Stuart Christine, De Paoli Silvia H, Simak Jan, Lin Tsai-Lien, Gao Yamei, Ovanesov Mikhail, Liang Yideng, Scott Dorothy, Brown Janice, Bai Yun, Metcalfe Dean D, Marszal Ewa, Ragheb Jack A
Office of Blood Research and Review, Center for Biologics Evaluation and Research, US Food and Drug Administration, Silver Spring, Maryland 20993.
Office of Biostatistics and Epidemiology, Center for Biologics Evaluation and Research, US Food and Drug Administration, Silver Spring, Maryland 20993.
J Pharm Sci. 2016 Mar;105(3):1023-7. doi: 10.1016/S0022-3549(15)00180-X. Epub 2016 Feb 3.
Peginesatide (Omontys(®); Affymax, Inc., Cupertino, CA) was voluntarily withdrawn from the market less than a year after the product launch. Although clinical trials had demonstrated the drug to be safe and efficacious, 49 cases of anaphylaxis, including 7 fatalities, were reported not long after market introduction. Commercialization was initiated with a multiuse vial presentation, which differs in formulation from the single-use vial presentation used in phase 3 studies. Standard physical and chemical testing did not indicate any deviation from product specifications in either formulation. However, an analysis of subvisible particulates using nanoparticle tracking analysis and flow imaging revealed a significantly higher concentration of subvisible particles in the multiuse vial presentation linked to the hypersensitivity cases. Although it is unknown whether the elevated particulate content is causally related to these serious adverse events, this report illustrates the utility of characterizing subvisible particulates not captured by conventional light obscuration.
聚乙二醇化促红细胞生成素(Omontys(®);Affymax公司,加利福尼亚州库比蒂诺)在产品上市不到一年后就被自愿撤出市场。尽管临床试验表明该药物安全有效,但在上市后不久就报告了49例过敏反应病例,其中7例死亡。商业化产品采用的是多剂量瓶包装,其配方与3期研究中使用的单剂量瓶包装不同。标准的物理和化学检测未显示任何一种配方与产品规格有偏差。然而,使用纳米颗粒跟踪分析和流动成像对亚可见颗粒进行的分析显示,与过敏反应病例相关的多剂量瓶包装中亚可见颗粒的浓度明显更高。尽管尚不清楚颗粒含量升高是否与这些严重不良事件存在因果关系,但本报告说明了表征传统光阻法未捕获的亚可见颗粒的作用。