Fang Yuan, Song Menghua, Pu Tianning, Song Xiaoqing, Xu Kailu, Shen Pengcheng, Cao Ting, Zhao Yiman, Hsu Simon, Han Dongmei, Huang Qiang
State Key Laboratory of Genetics and Development of Complex Phenotypes, Shanghai Engineering Research Center of Industrial Microorganisms, MOE Engineering Research Center of Gene Technology, School of Life Sciences, Fudan University, Shanghai, 200438, China.
Department of Technical Operations, Shanghai Henlius Biotech, Inc., Shanghai, 200233, China.
Adv Sci (Weinh). 2025 Jun;12(23):e2500004. doi: 10.1002/advs.202500004. Epub 2025 Apr 24.
VHHs (also known as nanobodies) are important therapeutic antibodies. To prolong their half-life in bloodstream, VHHs are usually fused to the Fc fragment of full-length antibodies. However, stability is often the main challenge for their commercialization, and methods to improve stability are still lacking. Here, an in silico pipeline is developed for analyzing the stability of an anticancer VHH-Fc fusion antibody (VFA01) and designing its stable variants. Computational modeling is used to analyze the VFA01 structure and evaluate its conformational stability, disulfide bond reduction state, and aggregation and degradation tendency. By building mechanistic models of aggregation and degradation, the hotspot residues affecting stability: C130, F57, Y106, L120, and W111 are identified. Based on them, a series of VFA01 variants are designed and obtained a variant M11 (C130S/W111F/F57K) whose stability is significantly enhanced compared to VFA01: there are no visible particles in solution, and the change rate of DLS average hydrodynamic size, SEC HMW%, and CE-SDS purity are improved by 6.2-, 3.4-, and 1.5-fold, respectively. Both antigen-binding activity and production yield are also improved by about 1.5-fold. The results show that our computational pipeline is a very promising approach for improving the protein stability of therapeutic VHH-Fc fusion antibodies.
VHH(也称为纳米抗体)是重要的治疗性抗体。为了延长其在血液中的半衰期,VHH通常与全长抗体的Fc片段融合。然而,稳定性往往是其商业化的主要挑战,且仍缺乏提高稳定性的方法。在此,开发了一种计算机模拟流程,用于分析一种抗癌VHH-Fc融合抗体(VFA01)的稳定性并设计其稳定变体。利用计算建模来分析VFA01的结构,并评估其构象稳定性、二硫键还原状态以及聚集和降解趋势。通过构建聚集和降解的机理模型,确定了影响稳定性的热点残基:C130、F57、Y106、L120和W111。基于这些残基,设计了一系列VFA01变体,并获得了一个变体M11(C130S/W111F/F57K),其稳定性与VFA01相比显著增强:溶液中无可见颗粒,动态光散射(DLS)平均流体力学尺寸、尺寸排阻色谱(SEC)高分子量(HMW)百分比和毛细管电泳-十二烷基硫酸钠(CE-SDS)纯度的变化率分别提高了6.2倍、3.4倍和1.5倍。抗原结合活性和产量也提高了约1.5倍。结果表明,我们的计算机模拟流程是提高治疗性VHH-Fc融合抗体蛋白质稳定性的一种非常有前景的方法。