用于隐性营养不良性大疱性表皮松解症的巨核酸酶介导的COL7A1基因校正 - Suppr

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Meganuclease-Mediated COL7A1 Gene Correction for Recessive Dystrophic Epidermolysis Bullosa.

作者信息

Izmiryan Araksya, Danos Olivier, Hovnanian Alain

机构信息

INSERM UMR, Imagine Institute, Paris, France; University Paris Descartes Sorbonne Cité, Paris, France.

Biogen, Cambridge, Massachusetts, USA.

出版信息

J Invest Dermatol. 2016 Apr;136(4):872-875. doi: 10.1016/j.jid.2015.11.028. Epub 2016 Feb 17.

DOI:10.1016/j.jid.2015.11.028

PMID:26897595

Abstract

摘要

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