LIN28B/let-7轴是多发性骨髓瘤中的一条新型治疗途径。
The LIN28B/let-7 axis is a novel therapeutic pathway in multiple myeloma.
作者信息
Manier S, Powers J T, Sacco A, Glavey S V, Huynh D, Reagan M R, Salem K Z, Moschetta M, Shi J, Mishima Y, Roche-Lestienne C, Leleu X, Roccaro A M, Daley G Q, Ghobrial I M
机构信息
Department of Medical Oncology, Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA, USA.
Service des Maladies du Sang, CHRU Lille, Lille, France.
出版信息
Leukemia. 2017 Apr;31(4):853-860. doi: 10.1038/leu.2016.296. Epub 2016 Oct 24.
MYC is a major oncogenic driver of multiple myeloma (MM) and yet almost no therapeutic agents exist that target MYC in MM. Here we report that the let-7 biogenesis inhibitor LIN28B correlates with MYC expression in MM and is associated with adverse outcome. We also demonstrate that the LIN28B/let-7 axis modulates the expression of MYC, itself a let-7 target. Further, perturbation of the axis regulates the proliferation of MM cells in vivo in a xenograft tumor model. RNA-sequencing and gene set enrichment analyses of CRISPR-engineered cells further suggest that the LIN28/let-7 axis regulates MYC and cell cycle pathways in MM. We provide proof of principle for therapeutic regulation of MYC through let-7 with an LNA-GapmeR (locked nucleic acid-GapmeR) containing a let-7b mimic in vivo, demonstrating that high levels of let-7 expression repress tumor growth by regulating MYC expression. These findings reveal a novel mechanism of therapeutic targeting of MYC through the LIN28B/let-7 axis in MM that may impact other MYC-dependent cancers as well.
MYC是多发性骨髓瘤(MM)的主要致癌驱动因素,但几乎不存在针对MM中MYC的治疗药物。在此我们报告,let-7生物合成抑制剂LIN28B与MM中的MYC表达相关,并与不良预后相关。我们还证明LIN28B/let-7轴调节MYC的表达,而MYC本身就是一个let-7靶点。此外,在异种移植肿瘤模型中,该轴的扰动调节了MM细胞在体内的增殖。对经CRISPR基因编辑的细胞进行RNA测序和基因集富集分析进一步表明,LIN28/let-7轴在MM中调节MYC和细胞周期通路。我们通过在体内使用含有let-7b模拟物的LNA-GapmeR(锁核酸-GapmeR),为通过let-7对MYC进行治疗性调节提供了原理证明,表明高水平的let-7表达通过调节MYC表达来抑制肿瘤生长。这些发现揭示了一种通过MM中的LIN28B/let-7轴对MYC进行治疗靶向的新机制,这可能也会影响其他MYC依赖性癌症。