文献检索文档翻译深度研究
Suppr Zotero 插件Zotero 插件
邀请有礼套餐&价格历史记录

新学期,新优惠

限时优惠:9月1日-9月22日

30天高级会员仅需29元

1天体验卡首发特惠仅需5.99元

了解详情
不再提醒
插件&应用
Suppr Zotero 插件Zotero 插件浏览器插件Mac 客户端Windows 客户端微信小程序
高级版
套餐订阅购买积分包
AI 工具
文献检索文档翻译深度研究
关于我们
关于 Suppr公司介绍联系我们用户协议隐私条款
关注我们

Suppr 超能文献

核心技术专利:CN118964589B侵权必究
粤ICP备2023148730 号-1Suppr @ 2025

全基因组规模的 CRISPR-Cas9 基因敲除筛选在人类细胞中的应用。

Genome-scale CRISPR-Cas9 knockout screening in human cells.

机构信息

Broad Institute of MIT and Harvard, 7 Cambridge Center, MA 02142, USA.

McGovern Institute for Brain Research, Department of Brain and Cognitive Sciences, Department of Biological Engineering, Massachusetts Institute of Technology, Cambridge, MA 02139, USA.

出版信息

Science. 2014 Jan 3;343(6166):84-87. doi: 10.1126/science.1247005. Epub 2013 Dec 12.


DOI:10.1126/science.1247005
PMID:24336571
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC4089965/
Abstract

The simplicity of programming the CRISPR (clustered regularly interspaced short palindromic repeats)-associated nuclease Cas9 to modify specific genomic loci suggests a new way to interrogate gene function on a genome-wide scale. We show that lentiviral delivery of a genome-scale CRISPR-Cas9 knockout (GeCKO) library targeting 18,080 genes with 64,751 unique guide sequences enables both negative and positive selection screening in human cells. First, we used the GeCKO library to identify genes essential for cell viability in cancer and pluripotent stem cells. Next, in a melanoma model, we screened for genes whose loss is involved in resistance to vemurafenib, a therapeutic RAF inhibitor. Our highest-ranking candidates include previously validated genes NF1 and MED12, as well as novel hits NF2, CUL3, TADA2B, and TADA1. We observe a high level of consistency between independent guide RNAs targeting the same gene and a high rate of hit confirmation, demonstrating the promise of genome-scale screening with Cas9.

摘要

CRISPR(成簇规律间隔短回文重复)相关核酸酶 Cas9 编程的简单性提示了一种在全基因组范围内研究基因功能的新方法。我们展示了慢病毒递送靶向 18080 个基因的全基因组 CRISPR-Cas9 敲除(GeCKO)文库,该文库包含 64751 个独特的指导序列,可在人类细胞中进行负筛选和正筛选。首先,我们使用 GeCKO 文库鉴定了对癌细胞和多能干细胞存活至关重要的基因。接下来,在黑色素瘤模型中,我们筛选了与 vemurafenib(一种治疗性 RAF 抑制剂)耐药相关的基因缺失。我们排名最高的候选基因包括先前验证的 NF1 和 MED12 基因,以及新的 NF2、CUL3、TADA2B 和 TADA1 基因。我们观察到针对同一基因的独立向导 RNA 之间具有高度一致性,并且命中确认率很高,这证明了 Cas9 进行全基因组筛选的潜力。

相似文献

[1]
Genome-scale CRISPR-Cas9 knockout screening in human cells.

Science. 2013-12-12

[2]
High-resolution interrogation of functional elements in the noncoding genome.

Science. 2016-9-30

[3]
Genome-scale transcriptional activation by an engineered CRISPR-Cas9 complex.

Nature. 2015-1-29

[4]
Identification of pathways modulating vemurafenib resistance in melanoma cells via a genome-wide CRISPR/Cas9 screen.

G3 (Bethesda). 2021-2-9

[5]
Genome-scale activation screen identifies a lncRNA locus regulating a gene neighbourhood.

Nature. 2017-8-17

[6]
Genetic screens in human cells using the CRISPR-Cas9 system.

Science. 2013-12-12

[7]
High-throughput screens in mammalian cells using the CRISPR-Cas9 system.

FEBS J. 2015-6

[8]
Mechanisms of resistance to RAF inhibitors in melanoma.

J Invest Dermatol. 2011-5-19

[9]
Genome-wide CRISPR screens reveal genetic mediators of cereblon modulator toxicity in primary effusion lymphoma.

Blood Adv. 2019-7-23

[10]
Revealing Temozolomide Resistance Mechanisms via Genome-Wide CRISPR Libraries.

Cells. 2020-12-1

引用本文的文献

[1]
Syncytial death mediated by oncolytic rVSV-NDV dynamically activates immunogenic apoptosis and necroptosis in human lung cancer cells.

Mol Ther Oncol. 2025-8-5

[2]
Revealing genetic drivers of ovarian cancer and chemoresistance: insights from whole-genome CRISPR-knockout library screens.

Cell Oncol (Dordr). 2025-8-28

[3]
Advances in Epstein-Barr Virus Detection: From Traditional Methods to Modern Technologies.

Viruses. 2025-7-22

[4]
Interaction of genetic variants activates latent metabolic pathways in yeast.

Nat Commun. 2025-8-27

[5]
CRISPR/Cas9 screening identifies SUV39H2 as a key regulator of oHSV-1 resistance in oral squamous cell carcinoma.

Cell Death Discov. 2025-8-23

[6]
Genome-wide in vivo CRISPR screens identify GATOR1 complex as a tumor suppressor in Myc-driven lymphoma.

Nat Commun. 2025-8-21

[7]
Synergistic effect of MDM2 inhibitors and radiotherapy in endometrial cancer.

NPJ Precis Oncol. 2025-8-18

[8]
The membrane-associated ubiquitin ligases MARCH2 and MARCH3 target TIM-1 to limit Zika virus infection.

Cell Mol Immunol. 2025-8-15

[9]
Genome Editing Breeding with CRISPR-Cas Nucleases, Base Editors, and Prime Editors.

Animals (Basel). 2025-7-22

[10]
Uridine as a hub in cancer metabolism and RNA biology.

Exp Mol Med. 2025-8-14

本文引用的文献

[1]
Double nicking by RNA-guided CRISPR Cas9 for enhanced genome editing specificity.

Cell. 2013-8-29

[2]
Advances in the treatment of neurofibromatosis-associated tumours.

Nat Rev Clin Oncol. 2013-8-13

[3]
CAS9 transcriptional activators for target specificity screening and paired nickases for cooperative genome engineering.

Nat Biotechnol. 2013-8-1

[4]
CRISPR RNA-guided activation of endogenous human genes.

Nat Methods. 2013-7-25

[5]
RNA-guided gene activation by CRISPR-Cas9-based transcription factors.

Nat Methods. 2013-7-25

[6]
Optical control of mammalian endogenous transcription and epigenetic states.

Nature. 2013-8-23

[7]
DNA targeting specificity of RNA-guided Cas9 nucleases.

Nat Biotechnol. 2013-7-21

[8]
CRISPR-mediated modular RNA-guided regulation of transcription in eukaryotes.

Cell. 2013-7-11

[9]
A genome-scale RNA interference screen implicates NF1 loss in resistance to RAF inhibition.

Cancer Discov. 2013-1-3

[10]
RNA-guided human genome engineering via Cas9.

Science. 2013-1-3

文献AI研究员

20分钟写一篇综述,助力文献阅读效率提升50倍

立即体验

用中文搜PubMed

大模型驱动的PubMed中文搜索引擎

马上搜索

推荐工具

医学文档翻译智能文献检索