Department of Chemical Engineering and Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, MA 02139, USA.
Cardiovascular Division, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA 02115, USA.
Sci Transl Med. 2016 Nov 16;8(365):365ra157. doi: 10.1126/scitranslmed.aag2374.
Efforts at elimination of scourges, such as malaria, are limited by the logistic challenges of reaching large rural populations and ensuring patient adherence to adequate pharmacologic treatment. We have developed an oral, ultra-long-acting capsule that dissolves in the stomach and deploys a star-shaped dosage form that releases drug while assuming a geometry that prevents passage through the pylorus yet allows passage of food, enabling prolonged gastric residence. This gastric-resident, drug delivery dosage form releases small-molecule drugs for days to weeks and potentially longer. Upon dissolution of the macrostructure, the components can safely pass through the gastrointestinal tract. Clinical, radiographic, and endoscopic evaluation of a swine large-animal model that received these dosage forms showed no evidence of gastrointestinal obstruction or mucosal injury. We generated long-acting formulations for controlled release of ivermectin, a drug that targets malaria-transmitting mosquitoes, in the gastric environment and incorporated these into our dosage form, which then delivered a sustained therapeutic dose of ivermectin for up to 14 days in our swine model. Further, by using mathematical models of malaria transmission that incorporate the lethal effect of ivermectin against malaria-transmitting mosquitoes, we demonstrated that this system will boost the efficacy of mass drug administration toward malaria elimination goals. Encapsulated, gastric-resident dosage forms for ultra-long-acting drug delivery have the potential to revolutionize treatment options for malaria and other diseases that affect large populations around the globe for which treatment adherence is essential for efficacy.
消除疟疾等祸害的努力受到向广大农村人口提供服务和确保患者坚持充分药物治疗的后勤挑战的限制。我们开发了一种口服、超长效胶囊,该胶囊在胃中溶解,并采用星形剂型释放药物,同时采用一种防止通过幽门但允许食物通过的几何形状,从而实现延长胃停留时间。这种胃驻留型药物输送剂型可使小分子药物持续释放数天至数周,甚至更长时间。在宏观结构溶解后,其成分可以安全地通过胃肠道。对接受这些剂型的猪大动物模型进行的临床、放射学和内镜评估未显示出胃肠道梗阻或粘膜损伤的证据。我们在胃环境中生成了伊维菌素的控释长效制剂,伊维菌素是一种针对传播疟疾的蚊子的药物,并将其纳入我们的剂型中,然后在我们的猪模型中持续 14 天提供伊维菌素的持续治疗剂量。此外,通过使用包含伊维菌素对传播疟疾的蚊子的致死作用的疟疾传播数学模型,我们证明该系统将提高大规模药物管理实现消除疟疾目标的效果。用于超长效药物输送的封装的胃驻留剂型有可能彻底改变对全球范围内影响大量人群的疟疾和其他疾病的治疗选择,因为这些疾病的治疗效果取决于患者的坚持性。