Baruteau J, Waddington S N, Alexander I E, Gissen P
Genetics and Genomic Medicine Programme, Great Ormond Street Institute of Child Health, University College London, London, UK.
Department of Metabolic Medicine, Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.
Gene Ther. 2017 May;24(5):263-264. doi: 10.1038/gt.2016.90. Epub 2017 Jan 12.