用基因疗法围剿镰状细胞。
Rounding up sickle cells with gene therapy.
机构信息
Department of Ophthalmology, University of Pittsburgh, Pittsburgh, PA 15213, USA. Email:
出版信息
Sci Transl Med. 2017 Mar 15;9(381). doi: 10.1126/scitranslmed.aam9864.
PMID:28298423
Abstract
A report of a patient treated with ex vivo lentiviral gene transfer to hematopoietic stem cells shows the promise of gene therapy for sickle cell anemia.
摘要
一份对接受体外慢病毒基因转导造血干细胞治疗的患者的报告显示，基因疗法治疗镰状细胞贫血症具有广阔的前景。
Zotero 插件