Rewcastle Gordon W, Kolekar Sharada, Buchanan Christina M, Gamage Swarna A, Giddens Anna C, Tsang Kit Y, Kendall Jackie D, Singh Ripudaman, Lee Woo-Jeong, Smith Greg C, Han Weiping, Matthews David J, Denny William A, Shepherd Peter R, Jamieson Stephen M F
Auckland Cancer Society Research Centre, School of Medical and Health Sciences, The University of Auckland, Auckland, New Zealand.
Maurice Wilkins Centre for Molecular Biodiscovery, The University of Auckland, Auckland, New Zealand.
Oncotarget. 2017 Jul 18;8(29):47725-47740. doi: 10.18632/oncotarget.17730.
Multiple therapeutic agents have been developed to target the phosphatidylinositol 3-kinase (PI3K) signaling pathway, which is frequently dysregulated in cancer promoting tumor growth and survival. These include pan PI3K inhibitors, which target class Ia PI3K isoforms and have largely shown limited single agent activity with narrow therapeutic windows in clinical trials. Here, we characterize SN32976, a novel pan PI3K inhibitor, for its biochemical potency against PI3K isoforms and mTOR, kinase selectivity, cellular activity, pharmacokinetics, pharmacodynamics and antitumor efficacy relative to five clinically-evaluated pan PI3K inhibitors: buparlisib, dactolisib, pictilisib, omipalisib and ZSTK474. SN32976 potently inhibited PI3K isoforms and mTOR, displaying preferential activity for PI3Kα and sparing of PI3Kδ relative to the other inhibitors, while showing less off-target activity than the clinical inhibitors in a panel of 442 kinases. The major metabolites of SN32976 were also potent PI3K inhibitors with similar selectivity for PI3Kα as the parent compound. SN32976 compared favorably with the clinically-evaluated PI3K inhibitors in cellular assays, inhibiting pAKT expression and cell proliferation at nM concentrations, and in animal models, inducing a greater extent and duration of pAKT inhibition in tumors than pictilisib, dactolisib and omipalisib at similarly tolerated dose levels and inhibiting tumor growth to a greater extent than dactolisib and ZSTK474 and with similar efficacy to pictilisib and omipalisib. These results suggest that SN32976 is a promising clinical candidate for cancer therapy with enhanced kinase selectivity and preferential inhibition of PI3Kα compared to first generation pan PI3K inhibitors, while retaining comparable anticancer activity.
已经开发了多种治疗药物来靶向磷脂酰肌醇3-激酶(PI3K)信号通路,该通路在促进肿瘤生长和存活的癌症中经常失调。这些药物包括泛PI3K抑制剂,其靶向I类a型PI3K亚型,并且在临床试验中大多显示出有限的单药活性和狭窄的治疗窗口。在此,我们对新型泛PI3K抑制剂SN32976进行了表征,测定了其对PI3K亚型和mTOR的生化活性、激酶选择性、细胞活性、药代动力学、药效学以及相对于五种临床评估的泛PI3K抑制剂(buparlisib、dactolisib、pictilisib、omipalisib和ZSTK474)的抗肿瘤疗效。SN32976有效抑制PI3K亚型和mTOR,相对于其他抑制剂,对PI3Kα表现出优先活性,对PI3Kδ的抑制作用较弱,同时在一组442种激酶中显示出比临床抑制剂更低的脱靶活性。SN32976的主要代谢产物也是有效的PI3K抑制剂,对PI3Kα的选择性与母体化合物相似。在细胞试验中,SN32976与临床评估的PI3K抑制剂相比表现良好,在纳摩尔浓度下抑制pAKT表达和细胞增殖;在动物模型中,在相似的耐受剂量水平下,与pictilisib、dactolisib和omipalisib相比,SN32976在肿瘤中诱导pAKT抑制的程度和持续时间更大,并且比dactolisib和ZSTK474更有效地抑制肿瘤生长,与pictilisib和omipalisib具有相似的疗效。这些结果表明,与第一代泛PI3K抑制剂相比,SN32976具有增强的激酶选择性和对PI3Kα的优先抑制作用,同时保留了相当的抗癌活性,是一种有前景的癌症治疗临床候选药物。