Niemeyer Charlotte M, Mecucci Cristina
Department of Pediatrics and Adolescent Medicine, Division of Pediatric Hematology and Oncology; Medical Center; Faculty of Medicine, University of Freiburg, Germany.
Hematology and Bone Marrow Transplantation Unit, University of Perugia, Perugia, Italy.
Semin Hematol. 2017 Apr;54(2):69-74. doi: 10.1053/j.seminhematol.2017.04.002. Epub 2017 Apr 6.
Newly diagnosed children and adults with myelodysplastic syndrome (MDS) or acute myeloid leukemia (AML) need to be screened for presence of a genetic predisposition syndrome because the information on the genetic status is likely to influence clinical care and management of the patient and the family. Scenarios in which genetic counseling is advised include presence of a mutation on somatic screen that can be associated with a germline predisposition, hematologic or cytogenetic characteristics suggestive of an underlying susceptibility syndrome, non-hematological phenotype suspicious for a familial condition, history of previous malignancy, or a family history of cancer, cytopenia, autoimmunity, or organ-system manifestation fitting a predisposition syndrome. With increasing complexity on phenotypes, genetics, and leukemia risk of the recently recognized predisposition syndromes, specialized clinics for hereditary hematologic malignancies have been initiated to guide genetic testing and support hematologists integrating genetic data into therapeutic strategies and clinical care. Recommendations for surveillance of carriers are currently based on expert opinion and subject to future modification when a more complete picture for the distinct genetic entities will arise.
新诊断的骨髓增生异常综合征(MDS)或急性髓系白血病(AML)儿童及成人患者需要进行遗传易感性综合征筛查,因为遗传状态信息可能会影响患者及其家庭的临床护理和管理。建议进行遗传咨询的情况包括:体细胞筛查存在可能与种系易感性相关的突变、提示潜在易感性综合征的血液学或细胞遗传学特征、怀疑为家族性疾病的非血液学表型、既往恶性肿瘤病史、或癌症、血细胞减少、自身免疫或符合易感性综合征的器官系统表现的家族史。随着最近认识到的易感性综合征的表型、遗传学和白血病风险日益复杂,已设立了遗传性血液系统恶性肿瘤专科门诊,以指导基因检测,并支持血液科医生将遗传数据整合到治疗策略和临床护理中。目前,对携带者监测的建议基于专家意见,当对不同遗传实体有更全面的了解时,可能会在未来进行修改。