High-titre inhibitors in previously untreated patients with severe haemophilia A receiving recombinant or plasma-derived factor VIII: a budget-impact analysis.
作者信息
Messori Andrea, Peyvandi Flora, Trippoli Sabrina, Palla Roberta, Rosendaal Frits R, Mannucci Pier Mannuccio
机构信息
HTA Unit, ESTAR, Regional Health Service, Florence, Italy.
"A. Bianchi Bonomi" Haemophilia and Thrombosis Centre, "Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico", Milan, Italy.
出版信息
Blood Transfus. 2018 Feb;16(2):215-220. doi: 10.2450/2017.0352-16. Epub 2017 May 15.
Abstract
摘要
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Reply to "High-titre inhibitors in previously untreated patients with severe haemophilia A receiving recombinant or plasma-derived factor VIII: a budget-impact analysis" by Messori et al.对梅索里等人《接受重组或血浆源性凝血因子 VIII 治疗的既往未治疗的重度甲型血友病患者中的高滴度抑制剂：预算影响分析》一文的回复
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Eur J Hosp Pharm. 2016 Jul;23(4):219-223. doi: 10.1136/ejhpharm-2015-000728. Epub 2015 Dec 23.
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A Randomized Trial of Factor VIII and Neutralizing Antibodies in Hemophilia A.A 随机对照试验VIII 因子和中和抗体在血友病 A.
N Engl J Med. 2016 May 26;374(21):2054-64. doi: 10.1056/NEJMoa1516437.
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Risk of inhibitors in previously untreated patients with hemophilia: a meta-analysis of literature studies.既往未经治疗的血友病患者中出现抑制物的风险：文献研究的荟萃分析
Blood. 2015 Jun 11;125(24):3819-21. doi: 10.1182/blood-2015-01-621383.
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J Gen Intern Med. 2014 Aug;29 Suppl 3(Suppl 3):S767-73. doi: 10.1007/s11606-014-2880-3.
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Purchasing factor concentrates in the 21st century through competitive tendering.21 世纪通过竞争性招标集中采购要素。
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Value Health. 2013 Mar-Apr;16(2):231-50. doi: 10.1016/j.jval.2013.02.002.
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