Should eliglustat be first line therapy for patients with type 1 Gaucher disease? Definitions of safety and efficacy.
作者信息
Zimran Ari, Goldblatt Jack, Szer Jeff
机构信息
Gaucher Clinic, Shaare Zedek Medical Center, 12 Bayit Street, Jerusalem 91031, Israel.
Genetics Services of Western Australia, 374 Bagot Rd, Subiaco, WA 6008, Australia.
出版信息
Blood Cells Mol Dis. 2018 Feb;68:14-16. doi: 10.1016/j.bcmd.2017.09.003. Epub 2017 Sep 14.
PMID:28935503
Abstract
摘要
Zotero 插件