Shi Jing, Darrah Erika, Sims Gary P, Mustelin Tomas, Sampson Kevon, Konig Maximilian F, Bingham Clifton O, Rosen Antony, Andrade Felipe
Division of Rheumatology, The Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
Respiratory, Inflammation, and Autoimmunity, MedImmune LLC, Gaithersburg, Maryland, USA.
Ann Rheum Dis. 2018 Jan;77(1):141-148. doi: 10.1136/annrheumdis-2017-211489. Epub 2017 Oct 25.
The citrullinating enzyme peptidylarginine deiminase type 4 (PAD4) is the target of a polyclonal group of autoantibodies in patients with rheumatoid arthritis (RA). A subgroup of such antibodies, initially identified by cross-reactivity with peptidylarginine deiminase type 3 (PAD3), is strongly associated with progression of radiographic joint damage and interstitial lung disease and has the unique ability to activate PAD4. The features of these antibodies in terms of their T cell-dependent origin, genetic characteristics and effect of individual antibody specificities on PAD4 function remain to be defined.
We used PAD4 tagged with the monomeric fluorescent protein mWasabi to isolate PAD4-specific memory B cells from anti-PAD4 positive patients with RA and applied single cell cloning technologies to obtain monoclonal antibodies.
Among 44 single B cells, we cloned five antibodies with PAD4-activating properties. Sequence analysis, germline reversion experiments and antigen specificity assays suggested that autoantibodies to PAD4 are not polyreactive and arise from PAD4-reactive precursors. Somatic mutations increase the agonistic activity of these antibodies at low calcium concentrations by facilitating their interaction with structural epitopes that modulate calcium-binding site 5 in PAD4.
PAD4-activating antibodies directly amplify a key process in disease pathogenesis, making them unique among other autoantibodies in RA. Understanding the molecular basis for their functionality may inform the design of future PAD4 inhibitors.
瓜氨酸化酶4型肽基精氨酸脱亚氨酶(PAD4)是类风湿关节炎(RA)患者中一组多克隆自身抗体的靶点。这类抗体的一个亚组最初通过与3型肽基精氨酸脱亚氨酶(PAD3)的交叉反应性得以鉴定,它与影像学关节损伤和间质性肺病的进展密切相关,并且具有激活PAD4的独特能力。这些抗体在T细胞依赖性起源、遗传特征以及个体抗体特异性对PAD4功能的影响方面的特征仍有待明确。
我们使用标记有单体荧光蛋白mWasabi的PAD4,从抗PAD4阳性的RA患者中分离出PAD4特异性记忆B细胞,并应用单细胞克隆技术获得单克隆抗体。
在44个单个B细胞中,我们克隆出了5种具有PAD4激活特性的抗体。序列分析、胚系回复突变实验和抗原特异性分析表明,针对PAD4的自身抗体并非多反应性的,而是源自对PAD4有反应性的前体。体细胞突变通过促进这些抗体与调节PAD4中钙结合位点5的结构表位的相互作用,在低钙浓度下增强了它们的激动活性。
激活PAD4的抗体直接放大了疾病发病机制中的一个关键过程,使其在RA的其他自身抗体中独树一帜。了解其功能的分子基础可能为未来PAD4抑制剂的设计提供思路。