University of Arkansas for Medical Sciences, Division of Endocrinology and Metabolism, 4301 W. Markham Street, Mail Slot #587, Little Rock, AR 72205.
Eur Cell Mater. 2017 Dec 5;34:341-364. doi: 10.22203/eCM.v034a21.
Disease-modifying osteoarthritis drugs (DMOADs) should reach their intra-tissue target sites at optimal doses for clinical efficacy. The dense, negatively charged matrix of cartilage poses a major hindrance to the transport of potential therapeutics. In this work, electrostatic interactions were utilised to overcome this challenge and enable higher uptake, full-thickness penetration and enhanced retention of dexamethasone (Dex) inside rabbit cartilage. This was accomplished by using the positively charged glycoprotein avidin as nanocarrier, conjugated to Dex by releasable linkers. Therapeutic effects of a single intra-articular injection of low dose avidin-Dex (0.5 mg Dex) were evaluated in rabbits 3 weeks after anterior cruciate ligament transection (ACLT). Immunostaining confirmed that avidin penetrated the full cartilage thickness and was retained for at least 3 weeks. Avidin-Dex suppressed injury-induced joint swelling and catabolic gene expression to a greater extent than free Dex. It also significantly improved the histological score of cell infiltration and morphogenesis within the periarticular synovium. Micro-computed tomography confirmed the reduced incidence and volume of osteophytes following avidin-Dex treatment. However, neither treatment restored the loss of cartilage stiffness following ACLT, suggesting the need for a combinational therapy with a pro-anabolic factor for enhancing matrix biosynthesis. The avidin dose used caused significant glycosaminoglycan (GAG) loss, suggesting the use of higher Dex : avidin ratios in future formulations, such that the delivered avidin dose could be much less than that shown to affect GAGs. This charge-based delivery system converted cartilage into a drug depot that could also be employed for delivery to nearby synovium, menisci and ligaments, enabling clinical translation of a variety of DMOADs.
治疗性关节炎药物(DMOADs)应在达到最佳临床疗效的剂量下到达其组织内靶点。软骨致密的带负电荷的基质对潜在治疗剂的输送构成了重大障碍。在这项工作中,利用静电相互作用克服了这一挑战,使地塞米松(Dex)在兔软骨内的摄取量更高、全厚度渗透和保留增强。这是通过使用带正电荷的糖蛋白亲和素作为纳米载体,并通过可释放的接头将 Dex 与之共轭来实现的。在 ACLT 后 3 周,通过单次关节内注射低剂量亲和素-Dex(0.5mg Dex)评估了其在兔中的治疗效果。免疫染色证实,亲和素穿透了整个软骨厚度,并至少保留了 3 周。与游离 Dex 相比,亲和素-Dex 更能抑制损伤引起的关节肿胀和分解代谢基因表达。它还显著改善了关节周围滑膜内细胞浸润和形态发生的组织学评分。微计算机断层扫描证实,亲和素-Dex 治疗后骨赘的发生率和体积降低。然而,两种治疗方法都没有恢复 ACLT 后软骨刚度的丧失,这表明需要与促进基质生物合成的促合成代谢因子联合治疗。使用的亲和素剂量导致糖胺聚糖(GAG)大量丢失,这表明在未来的制剂中需要使用更高的 Dex:亲和素比,以便输送的亲和素剂量可以远远低于影响 GAG 的剂量。这种基于电荷的输送系统将软骨转化为药物库,也可用于向附近的滑膜、半月板和韧带输送,从而实现各种治疗性关节炎药物的临床转化。