Hematopoietic stem cell transplantation for patients with paroxysmal nocturnal hemoglobinuria previously treated with eculizumab: a retrospective study of 21 patients from SFGM-TC centers.
作者信息
Vallet Nicolas, de Fontbrune Flore Sicre, Loschi Michaël, Desmier Deborah, Villate Alban, Barraco Fiorenza, Chevallier Patrice, Terriou Louis, Yakoub-Agha Ibrahim, Ruggeri Annalisa, Mohty Mohamad, Maillard Natacha, Rohrlich Pierre-Simon, Ceballos Patrice, Nguyen Stéphanie, Poiré Xavier, Guillerm Gaëlle, Tabrizi Reza, Farhi Jonathan, Devillier Raynier, Rubio Marie-Thérèse, Socié Gérard, de Latour Régis Peffault
机构信息
Hematology Department, Tours, France.
Hematology Department, Saint Louis Hospital, Paris, France.
出版信息
Haematologica. 2018 Mar;103(3):e103-e105. doi: 10.3324/haematol.2017.182360. Epub 2017 Dec 21.
Abstract
摘要
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Impact of eculizumab treatment on paroxysmal nocturnal hemoglobinuria: a treatment versus no-treatment study.依库珠单抗治疗对阵发性睡眠性血红蛋白尿症的影响：一项治疗与未治疗研究。
Am J Hematol. 2016 Jun;91(4):366-70. doi: 10.1002/ajh.24278.
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Paroxysmal nocturnal hemoglobinuria.阵发性睡眠性血红蛋白尿症。
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Haematologica. 2012 Nov;97(11):1666-73. doi: 10.3324/haematol.2012.062828. Epub 2012 Jun 11.
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Long-term treatment with eculizumab in paroxysmal nocturnal hemoglobinuria: sustained efficacy and improved survival.依库珠单抗长期治疗阵发性睡眠性血红蛋白尿症：疗效持续且生存改善。
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