Department of Pharmacy, School of Chemical Sciences and Pharmacy , Central University of Rajasthan , Bandar Sindri , Distt. Ajmer , Rajasthan , India 305817.
Division of Pharmaceutics, University Institute of Pharmaceutical Sciences , Panjab University , Chandigarh , India 160014.
ACS Chem Neurosci. 2018 May 16;9(5):1152-1158. doi: 10.1021/acschemneuro.7b00519. Epub 2018 Feb 1.
Multiple sclerosis (MS) is a neurodegenerative disease in which myelin sheath damage occurs due to internal and external factors. MS especially affects the young population. Dimethyl fumarate (DMF) is a promising agent for MS treatment, although it is associated with concerns such as poor brain permeation, multiple dosing, and gastrointestinal flushing. The present study attempts to evaluate the preclinical performance of specially designed DMF-based lipoidal nanoparticles in a cuprizone-induced demyelination model in rodents. The studies proved the efficacy of lipid-based nanoparticles containing DMF in a once-a-day dosage regimen over that of thrice-a-day plain DMF administration on crucial parameters like motor coordination, grip strength, mortality, body weight, and locomotor activity. However, neither blank lipid nor blank neuroprotective (vitamins A, D, and E) loaded nanoparticles were able to elicit any desirable behavioral response. Histopathological studies showed that the designed once-a-day DMF nanomedicines were well tolerated and rejuvenated the myelin sheath vis-à-vis the plain DMF thrice-a-day regimen. These findings provide proof of concept for a biocompatible nanomedicine for MS with tremendous promise for effective brain delivery and patient compliance on the grounds of a reduction in the dosage frequency.
多发性硬化症 (MS) 是一种神经退行性疾病,其髓鞘损伤是由内部和外部因素引起的。多发性硬化症尤其影响年轻人群。富马酸二甲酯 (DMF) 是一种有前途的多发性硬化症治疗药物,但它与脑渗透不良、多次给药和胃肠道冲洗等问题有关。本研究试图评估在杯状朊病毒诱导的脱髓鞘模型中专门设计的基于 DMF 的脂质纳米粒子的临床前性能。研究证明,脂质纳米粒子含有 DMF 的每日一次剂量方案优于每日三次普通 DMF 给药方案,在运动协调、握力、死亡率、体重和运动活性等关键参数上更有效。然而,空白脂质或空白神经保护(维生素 A、D 和 E)负载的纳米粒子都不能引起任何理想的行为反应。组织病理学研究表明,设计的每日一次 DMF 纳米药物具有良好的耐受性,并使髓鞘鞘相对于每日三次普通 DMF 方案得到恢复。这些发现为多发性硬化症的生物相容性纳米药物提供了概念验证,具有巨大的有效脑部递药和提高患者顺应性的潜力,因为减少了用药频率。