Departments of Hematopathology.
Leukemia, The University of Texas MD Anderson Cancer Center, Houston, TX.
Am J Surg Pathol. 2018 Jun;42(6):799-806. doi: 10.1097/PAS.0000000000001058.
A subset of patients with chronic myelomonocytic leukemia (CMML) presents with significance myelofibrosis. In myelodysplastic syndromes, significant myelofibrosis has been associated with adverse outcomes and p53 dysregulation. However, in CMML the clinical and molecular correlates of significant myelofibrosis at presentation remain poorly understood. From a cohort of 651 CMML patients, we identified retrospectively 20 (3.1%) cases with moderate to severe reticulin fibrosis (CMML-F) detected at diagnosis, and we compared them to CMML patients without fibrosis (n=631) seen during the same period. Patients with CMML-F had a median age of 69.8 years (range, 24.8 to 91.2 y) and most (13; 65%) were men. Patients with CMML-F differed significantly from other CMML patients across the following parameters: white blood count, absolute monocyte count, serum lactate dehydrogenase level, splenomegaly, and bone marrow blast percentage. Notably, the frequency of JAK2 p.V617F mutation was higher in CMML-F patients compared with other CMML patients (P<0.001). Most CMML-F patients (12/20; 60%) had myeloproliferative CMML. Dysregulation of p53 was uncommon in CMML-F. CMML-F patients tended to have a shorter median overall survival compared with other CMML patients (P=0.079). Multivariate analysis using the Cox proportional hazards model showed an independent association between CMML-F and overall survival (P=0.047). In summary, unlike typical CMML, CMML-F is commonly associated with JAK2 p.V617F. The high frequency of myeloproliferative features and JAK2 p.V617F mutation, and the low frequency of p53 dysregulation, suggest that fibrosis in the context of CMML has a different pathogenesis from that previously reported in myelodysplastic syndrome.
一组慢性髓单核细胞白血病(CMML)患者存在显著的骨髓纤维化。在骨髓增生异常综合征中,显著的骨髓纤维化与不良预后和 p53 失调有关。然而,在 CMML 中,发病时显著骨髓纤维化的临床和分子相关性仍知之甚少。在 651 例 CMML 患者的队列中,我们回顾性地确定了 20 例(3.1%)在诊断时检测到中度至重度网状纤维纤维化(CMML-F)的病例,并将其与同期未纤维化的 CMML 患者(n=631)进行了比较。CMML-F 患者的中位年龄为 69.8 岁(范围,24.8 至 91.2 岁),大多数(13 例;65%)为男性。CMML-F 患者与其他 CMML 患者在以下参数上存在显著差异:白细胞计数、绝对单核细胞计数、血清乳酸脱氢酶水平、脾肿大和骨髓原始细胞百分比。值得注意的是,CMML-F 患者 JAK2 p.V617F 突变的频率明显高于其他 CMML 患者(P<0.001)。大多数 CMML-F 患者(12/20;60%)患有骨髓增生性 CMML。CMML-F 患者的 p53 失调并不常见。CMML-F 患者的总生存中位数明显短于其他 CMML 患者(P=0.079)。使用 Cox 比例风险模型的多变量分析显示,CMML-F 与总生存之间存在独立关联(P=0.047)。总之,与典型的 CMML 不同,CMML-F 通常与 JAK2 p.V617F 相关。骨髓增生特征和 JAK2 p.V617F 突变的高频率,以及 p53 失调的低频率,表明 CMML 背景下的纤维化与以前在骨髓增生异常综合征中报道的纤维化具有不同的发病机制。