Center for Reproductive Medicine, Amsterdam Research Institute Reproduction and Development, Academic Medical Centre, University of Amsterdam, Meibergdreef 9, 1105 AZ Amsterdam, The Netherlands.
Department of Obstetrics and Gynaecology, Amsterdam Reproduction and Development Research Institute, Academic Medical Centre, Meibergdeef 9, 1105 AZ, Amsterdam, The Netherlands.
Hum Reprod. 2018 May 1;33(5):784-792. doi: 10.1093/humrep/dey070.
In medicine, safety and efficacy are the two pillars on which the implementation of novel treatments rest. To protect the patient from unnecessary or unsafe treatments, usually, a stringent path of (pre) clinical testing is followed before a treatment is introduced into routine patient care. However, in reproductive medicine several techniques have been clinically introduced without elaborate preclinical studies. Moreover, novel reproductive techniques may harbor safety risks not only for the patients undergoing treatment, but also for the offspring conceived through these techniques. If preclinical (animal) studies were performed, efficacy and functionality the upper hand. When a new medically assisted reproduction (MAR) treatment was proven effective (i.e. if it resulted in live birth) the treatment was often rapidly implemented in the clinic. For IVF, the first study on the long-term health of IVF children was published a decade after its clinical implementation. In more recent years, prospective follow-up studies have been conducted that provided the opportunity to study the health of large groups of children derived from different reproductive techniques. Although such studies have indicated differences between children conceived through MAR and children conceived naturally, results are often difficult to interpret due to the observational nature of these studies (and the associated risk of confounding factors, e.g. subfertility of the parents), differences in definitions of clinical outcome measures, lack of uniformity in assessment protocols and heterogeneity of the underlying reasons for fertility treatment. With more novel MARs waiting at the horizon, there is a need for a framework on how to assess safety of novel reproductive techniques in a preclinical (animal) setting before they are clinically implemented. In this article, we provide a blueprint for preclinical testing of safety and health of offspring generated by novel MARs using a mouse model involving an array of tests that comprise the entire lifespan. We urge scientists to perform the proposed extensive preclinical tests for novel reproductive techniques with the goal to acquire knowledge on efficacy and the possible health effects of to-be implemented reproductive techniques to safeguard quality of novel MARs.
在医学领域,安全性和有效性是新型治疗方法实施的两个支柱。为了保护患者免受不必要或不安全的治疗,通常在将治疗方法引入常规患者护理之前,会进行严格的(临床前)测试路径。然而,在生殖医学中,有几种技术已经在临床中引入,而没有进行精心的临床前研究。此外,新型生殖技术不仅可能对接受治疗的患者存在安全风险,而且可能对通过这些技术受孕的后代存在安全风险。如果进行了临床前(动物)研究,则以疗效和功能为主。当一种新的辅助生殖治疗方法被证明有效(即,如果它导致活产)时,该治疗方法通常会迅速在临床上实施。对于体外受精(IVF),其临床实施十年后才发表了第一项关于 IVF 儿童长期健康的研究。近年来,进行了前瞻性随访研究,为研究来自不同生殖技术的大量儿童的健康提供了机会。尽管这些研究表明了通过 MAR 受孕的儿童与自然受孕的儿童之间存在差异,但由于这些研究的观察性质(以及相关的混杂因素风险,例如父母的生育能力低下)、临床结果衡量标准的定义差异、评估协议缺乏一致性以及生育治疗的根本原因的异质性,结果往往难以解释。随着更多新型 MAR 的出现,需要有一个框架,以便在临床实施之前,在临床前(动物)环境中评估新型生殖技术的安全性。在本文中,我们使用涉及一系列测试的小鼠模型,为新型 MAR 后代的安全性和健康提供了临床前测试的蓝图,这些测试涵盖了整个生命周期。我们敦促科学家对新型生殖技术进行拟议的广泛临床前测试,以获得关于即将实施的生殖技术的疗效和可能的健康影响的知识,从而保障新型 MAR 的质量。