X连锁肾上腺脑白质营养不良的新生儿筛查与新兴疗法 - Suppr

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Newborn Screening and Emerging Therapies for X-Linked Adrenoleukodystrophy.

作者信息

Moser Ann B, Fatemi Ali

机构信息

Kennedy Krieger Institute, Baltimore, Maryland.

出版信息

JAMA Neurol. 2018 Oct 1;75(10):1175-1176. doi: 10.1001/jamaneurol.2018.1585.

DOI:10.1001/jamaneurol.2018.1585

PMID:29946687

Abstract

摘要

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