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成年期诊断的短指智力发育迟缓综合征

Brachydactyly Mental Retardation Syndrome Diagnosed in Adulthood.

作者信息

Mahendhar Rupak, Zarghamravanbakhsh Paria, Pavlovic Maia Natalia, Butuc Radu, Sachmechi Issac

机构信息

Internal Medicine, Icahn School of Medicine at Mount Sinai/Queens Hospital Center, New York, USA.

Endocrinology, Icahn School of Medicine at Mount Sinai Queens Hospital Center, New York, USA.

出版信息

Cureus. 2018 Aug 21;10(8):e3169. doi: 10.7759/cureus.3169.

Abstract

Brachydactyly mental retardation syndrome (BDMR) is due to a rare, small chromosomal deletion of 2q37, and manifests with variable signs and symptoms in people who live with it. BDMR could be misdiagnosed as Albright hereditary osteodystrophy (AHO), because it presents with lack of hormone resistance to parathyroid hormone (PTH) and similar skeletal and craniofacial abnormalities; however, BDMR is far rarer and can present with a different phenotype. In some cases, BDMR patients exhibit malformations of the internal organs, which could cause life-threatening health issues. Associations have also been made between this chromosomal deletion and autism as well. We here report a case of BDMR with an AHO-like phenotype: mild mental retardation, along with normal calcium, phosphate, and PTH levels. Since our patient had a normal biochemical test, we considered pseudopseudohypoparathyroidism (PPHP) as the diagnosis and genetic testing was performed. Karyotype analysis showed deletion of the long q-arm of chromosome 2 in all analyzed cells-46 XX, del (2)(q37.1), which was consistent with BDMR. This deletion is a loss of around 100 genes that can present itself in various ways neurologically and physiologically, depending on the genes lost. However, because patients experience a range of symptoms such as autism, seizures, heart defects, brachydactyly, there could be unforeseen complications with BDMR. Therefore, we postulate that it is necessary to consider a diagnosis of BDMR in adults with AHO-like phenotype and normal calcium metabolism.

摘要

短指智力发育迟缓综合征(BDMR)是由2q37区域罕见的小染色体缺失引起的,患病个体表现出多种不同的体征和症状。BDMR可能会被误诊为奥尔布赖特遗传性骨营养不良(AHO),因为它表现出对甲状旁腺激素(PTH)缺乏激素抵抗以及类似的骨骼和颅面异常;然而,BDMR更为罕见,且可能呈现不同的表型。在某些情况下,BDMR患者会出现内脏畸形,这可能导致危及生命的健康问题。这种染色体缺失还与自闭症有关。我们在此报告一例具有AHO样表型的BDMR病例:轻度智力发育迟缓,同时钙、磷和PTH水平正常。由于我们的患者生化检查正常,我们最初考虑诊断为假性假性甲状旁腺功能减退症(PPHP)并进行了基因检测。核型分析显示所有分析细胞中染色体2的长臂q缺失——46 XX,del(2)(q37.1),这与BDMR一致。这种缺失约100个基因,根据所丢失的基因不同,在神经和生理方面会以各种方式表现出来。然而,由于患者会出现一系列症状,如自闭症、癫痫、心脏缺陷、短指,BDMR可能会有不可预见的并发症。因此,我们推测对于具有AHO样表型且钙代谢正常的成年人,有必要考虑BDMR的诊断。

https://cdn.ncbi.nlm.nih.gov/pmc/blobs/bd10/6197535/c2cd8b191372/cureus-0010-00000003169-i01.jpg

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