Pediatric and Congenital Cardiology Department, M3C Regional Reference CHD Center, CHU Montpellier, Montpellier, France; PHYMEDEXP, University of Montpellier, CNRS, INSERM, CHU Montpellier, Montpellier, France.
Pediatric and Congenital Cardiology Department, M3C Regional Reference CHD Center, CHU Montpellier, Montpellier, France; PHYMEDEXP, University of Montpellier, CNRS, INSERM, CHU Montpellier, Montpellier, France; Pediatric Cardiology and Rehabilitation Unit, St-Pierre Institute, Palavas-Les-Flots, France.
J Am Soc Echocardiogr. 2019 Mar;32(3):412-422. doi: 10.1016/j.echo.2018.10.017. Epub 2019 Jan 21.
Prognosis of Duchenne muscular dystrophy (DMD) is related to cardiac dysfunction. Speckle-tracking echocardiographic (STE) imaging is emerging as a noninvasive functional biomarker to consider in the early detection of DMD-related cardiomyopathy. However, STE analysis has not been assessed in a prospectively controlled study, especially in presymptomatic children with DMD, and no study has used STE analysis in all three displacements (longitudinal, radial, and circumferential) and for both ventricles.
This prospective controlled study enrolled 108 boys, 36 of whom had DMD (mean age, 11 ± 3.8 years) and 72 of whom were age-matched control subjects in a 1:2 case-control design. Conventional echocardiographic variables were collected for the left and right ventricles. STE analyses were performed in the longitudinal, radial, and circumferential displacements for the left ventricle and in the free wall longitudinal displacement for the right ventricle. The effect of age on the evolution of two-dimensional strain in children with DMD was studied by adding an interaction term, DMD × age, in the models.
Conventional echocardiographic measures were normal in both groups. Left ventricular (LV) ejection fraction ranged from 45% to 76% (mean, 63 ± 6%) in the DMD group and from 55% to 76% (mean, 64 ± 5%) in the control group. Global LV strain mean measures were significantly worse in the DMD group for the longitudinal (-16.8 ± 3.9% vs -20.6 ± 2.6%, P < .0001), radial (22.7 ± 11.3% vs 31.7 ± 14%, P = .002), and circumferential (-16.5 ± 3.8% vs -20.3 ± 3.1%, P < .0001) displacements. The decrease of global LV longitudinal strain with age in children with DMD was 0.34% per year more marked than that in control subjects. The LV inferolateral and anterolateral segments were specifically impaired, especially in the basal area. Right ventricular function evaluated using conventional echocardiography and STE analysis was normal and not different between children with DMD and control subjects.
The existence of altered LV strain despite normal LV function in children with DMD represents an important perspective for future pediatric drug trials in DMD-related cardiomyopathy prevention.
杜氏肌营养不良症(DMD)的预后与心脏功能障碍有关。斑点追踪超声心动图(STE)成像作为一种非侵入性的功能生物标志物,在早期发现 DMD 相关心肌病方面具有重要的应用价值。然而,STE 分析尚未在前瞻性对照研究中得到评估,尤其是在无症状的 DMD 患儿中,也没有研究使用 STE 分析对所有三个方向(纵向、径向和圆周向)和两个心室进行分析。
本前瞻性对照研究纳入了 108 名男孩,其中 36 名为 DMD 患儿(平均年龄 11 ± 3.8 岁),72 名为年龄匹配的对照组患儿,采用 1:2 的病例对照设计。采集左、右心室的常规超声心动图变量。STE 分析分别在左心室的纵向、径向和圆周向以及右心室的游离壁纵向位移进行。通过在模型中添加 DMD×年龄交互项,研究年龄对 DMD 患儿二维应变演变的影响。
两组的常规超声心动图指标均正常。DMD 组左心室(LV)射血分数范围为 45%至 76%(平均 63 ± 6%),对照组为 55%至 76%(平均 64 ± 5%)。DMD 组的整体 LV 应变平均测量值在纵向(-16.8 ± 3.9%比-20.6 ± 2.6%,P <.0001)、径向(22.7 ± 11.3%比 31.7 ± 14%,P =.002)和圆周向(-16.5 ± 3.8%比-20.3 ± 3.1%,P <.0001)方向均显著较差。DMD 患儿的整体 LV 纵向应变随年龄的下降速度比对照组快 0.34%/年。LV 下侧壁和前侧壁节段特别受损,尤其是基底段。使用常规超声心动图和 STE 分析评估的右心室功能正常,且在 DMD 患儿和对照组之间无差异。
尽管 DMD 患儿的左心室功能正常,但存在左心室应变改变,这为未来 DMD 相关心肌病预防的儿科药物试验提供了重要视角。