Queens College of the City University of New York, Chemistry and Biochemistry Department, 65-30 Kissena Blvd, Flushing, NY 11367-1597, USA; Chemistry Doctoral Program, The Graduate Center of the City University of New York, 365 5th Ave, New York, NY 10016, USA.
Queens College of the City University of New York, Department of Biology, 65-30 Kissena Blvd, Flushing, NY 11367-1597, USA.
Bioorg Chem. 2019 Apr;85:505-514. doi: 10.1016/j.bioorg.2019.02.032. Epub 2019 Feb 14.
Human cathepsin L is a ubiquitously expressed endopeptidase and is known to play critical roles in a wide variety of cellular signaling events. Its overexpression has been implicated in numerous human diseases, including highly invasive forms of cancer. Inhibition of cathepsin L is therefore considered a viable therapeutic strategy. Unfortunately, several redundant and even opposing roles of cathepsin L have recently emerged. Selective cathepsin L probes are therefore needed to dissect its function in context-specific manner before significant resources are directed into drug discovery efforts. Herein, the development of a clickable and tagless activity-based probe of cathepsin L is reported. The probe is highly efficient, active-site directed and activity-dependent, selective, cell penetrable, and non-toxic to human cells. Using zebrafish model, we demonstrate that the probe can inhibit cathepsin L function in vivo during the hatching process. It is anticipated that the probe will be a highly effective tool in dissecting cathepsin L biology at the proteome levels in both normal physiology and human diseases, thereby facilitating drug-discovery efforts targeting cathepsin L.
人组织蛋白酶 L 是一种广泛表达的内肽酶,已知在多种细胞信号事件中发挥关键作用。其过表达与许多人类疾病有关,包括高度侵袭性的癌症。因此,抑制组织蛋白酶 L 被认为是一种可行的治疗策略。不幸的是,组织蛋白酶 L 的几个冗余甚至相反的作用最近出现了。在将大量资源投入药物发现之前,需要选择性的组织蛋白酶 L 探针来以特定于上下文的方式剖析其功能。在此,报告了一种可点击且无标签的组织蛋白酶 L 活性基探针的开发。该探针高效、活性位点定向和依赖于活性、选择性、细胞可渗透且对人细胞无毒。使用斑马鱼模型,我们证明该探针可以在孵化过程中抑制体内的组织蛋白酶 L 功能。预计该探针将成为在正常生理和人类疾病中在蛋白质组水平上剖析组织蛋白酶 L 生物学的有效工具,从而促进针对组织蛋白酶 L 的药物发现。