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What compassionate use means for gene therapies.

作者信息

Chapman Carolyn Riley, Moch Kenneth I, McFadyen Andrew, Kearns Lisa, Watson Tom, Furlong Pat, Bateman-House Alison

机构信息

Division of Medical Ethics, Department of Population Health, NYU School of Medicine, New York, NY, USA.

Cognition Therapeutics, Pittsburgh, PA, USA.

出版信息

Nat Biotechnol. 2019 Apr;37(4):352-355. doi: 10.1038/s41587-019-0081-7.

DOI:10.1038/s41587-019-0081-7
PMID:30940936
Abstract
摘要

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