Engineering Research Center of Molecular and Neuro Imaging, Ministry of Education, School of Life Science and Technology , Xidian University , Xi'an 710071 , China.
Institute of Medical Research , Northwestern Polytechnical University , Xi'an 710072 , China.
Anal Chem. 2019 Oct 1;91(19):12392-12398. doi: 10.1021/acs.analchem.9b02935. Epub 2019 Sep 10.
Pre-mRNA splicing in the information exchange from DNA to protein is a critical step in all eukaryotes. However, there is currently a lack of noninvasive approaches for monitoring mRNA splicing events in cells. In this study, we presented a genetically encoded bioluminescence reporter, Rluc-intron, for noninvasive real-time monitoring the pre-mRNA splicing process in living cells and animals. It was designed by inserting a renilla luciferase (Rluc) gene into an intron sequence manipulated by RNA splicing modulator. We demonstrated that the splicing reporter Rluc-intron could provide real-time and quantitative information on the splicing activity responded to extracellular stimuli in living cells. In addition, Rluc-intron reporter is able to successfully quantify and image the pre-mRNA splicing in living mice in a noninvasive and longitudinal manner. This bioluminescence reporter provides the advantageous properties of systematic discovery of splicing modulators, which give the advances in pharmacogenomics and would produce new approach in the therapy of human diseases caused by splicing disorder.
在所有真核生物中,mRNA 的剪接是从 DNA 到蛋白质的信息交换的一个关键步骤。然而,目前还缺乏非侵入性的方法来监测细胞中的 mRNA 剪接事件。在这项研究中,我们提出了一种遗传编码的生物发光报告基因 Rluc-intron,用于非侵入性实时监测活细胞和动物中的前 mRNA 剪接过程。它是通过将海肾荧光素酶(Rluc)基因插入到受 RNA 剪接调节剂调控的内含子序列中设计而成的。我们证明,剪接报告基因 Rluc-intron 可以提供实时和定量的信息,反映细胞外刺激对剪接活性的影响。此外,Rluc-intron 报告基因能够成功地以非侵入性和纵向的方式定量和成像活小鼠中的前 mRNA 剪接。这种生物发光报告基因提供了系统性发现剪接调节剂的优势特性,这将推动药物基因组学的发展,并为因剪接紊乱导致的人类疾病的治疗提供新的方法。