Department of Biosciences, Biotechnologies and Biopharmaceutics, University of Bari, 70125 Bari, Italy.
Palladio Biosciences, Inc., Newtown, PA 18940, USA.
Int J Mol Sci. 2019 Dec 26;21(1):183. doi: 10.3390/ijms21010183.
Vasopressin V2 receptor (V2R) antagonists (vaptans) are a new generation of diuretics. Compared with classical diuretics, vaptans promote the excretion of retained body water in disorders in which plasma vasopressin concentrations are inappropriately high for any given plasma osmolality. Under these conditions, an aquaretic drug would be preferable over a conventional diuretic. The clinical efficacy of vaptans is in principle due to impaired vasopressin-regulated water reabsorption via the water channel aquaporin-2 (AQP2). Here, the effect of lixivaptan-a novel selective V2R antagonist-on the vasopressin-cAMP/PKA signaling cascade was investigated in mouse renal collecting duct cells expressing AQP2 (MCD4) and the human V2R. Compared to tolvaptan-a selective V2R antagonist indicated for the treatment of clinically significant hypervolemic and euvolemic hyponatremia-lixivaptan has been predicted to be less likely to cause liver injury. In MCD4 cells, clinically relevant concentrations of lixivaptan (100 nM for 1 h) prevented dDAVP-induced increase of cytosolic cAMP levels and AQP2 phosphorylation at ser-256. Consistent with this finding, real-time fluorescence kinetic measurements demonstrated that lixivaptan prevented dDAVP-induced increase in osmotic water permeability. These data represent the first detailed demonstration of the central role of AQP2 blockade in the aquaretic effect of lixivaptan and suggest that lixivaptan has the potential to become a safe and effective therapy for the treatment of disorders characterized by high plasma vasopressin concentrations and water retention.
加压素 V2 受体(V2R)拮抗剂(vaptans)是新一代利尿剂。与经典利尿剂相比,vaptans 促进了在血浆加压素浓度对于任何给定的血浆渗透压不适当高的情况下保留的体内水的排泄。在这些条件下,与传统利尿剂相比,水通道利尿剂可能更可取。vaptans 的临床疗效原则上归因于通过水通道 aquaporin-2(AQP2)受损的加压素调节的水重吸收。在这里,研究了新型选择性 V2R 拮抗剂 lixivaptan 对表达 AQP2(MCD4)和人 V2R 的小鼠肾集合管细胞中的加压素-cAMP/PKA 信号级联的影响。与用于治疗临床上显著的高容量和等容量低钠血症的选择性 V2R 拮抗剂 tolvaptan 相比,lixivaptan 不太可能引起肝损伤。在 MCD4 细胞中,临床相关浓度的 lixivaptan(100 nM,1 h)可预防 dDAVP 诱导的细胞浆 cAMP 水平和 AQP2 丝氨酸-256 磷酸化增加。与这一发现一致,实时荧光动力学测量表明,lixivaptan 可防止 dDAVP 诱导的渗透水通透性增加。这些数据代表了首次详细证明 AQP2 阻断在 lixivaptan 的 aquaretic 作用中的核心作用,并表明 lixivaptan 有可能成为治疗以高血浆加压素浓度和水潴留为特征的疾病的安全有效治疗方法。