Department of Internal Medicine, Division of Metabolism, Endocrinology & Diabetes, University of Michigan, 1150 West Medical Center Drive, Ann Arbor, MI, 48109, USA.
Clinical Research Division, Fred Hutchinson Cancer Research Center, Seattle, WA, USA.
Horm Cancer. 2020 Feb;11(1):52-62. doi: 10.1007/s12672-019-00375-0. Epub 2020 Jan 30.
Primary aldosteronism (PA) is the most common cause of secondary hypertension with a high prevalence among patients with resistant hypertension. Despite the recent discovery of somatic variants in aldosterone-producing adenoma (APA)-associated PA, causes for PA due to bilateral aldosterone production (bilateral hyperaldosteronism; BHA) remain unknown. Herein, we identified rare gene variants in ATP2B4, in a cohort of patients with BHA. ATP2B4 belongs to the same family of Ca-ATPases as ATP2B3, which is involved in the pathogenesis of APA. Endogenous ATP2B4 expression was characterized in adrenal tissue, and the gene variants were functionally analyzed for effects on aldosterone synthase (CYP11B2) expression, steroid production in basal and agonist-stimulated conditions, and for changes in biophysical properties of channel properties. Knockdown of ATP2B4 in HAC15 exhibited reduced angiotensin II stimulation in one of four shRNA clones. Stable HAC15 cell lines with doxycycline (dox) - inducible wild-type and variant forms of ATP2B4 - were generated, and dox-induced upregulation of ATP2B4 mRNA and protein was confirmed. However, ATP2B4 variants did not alter basal or agonist-stimulated CYP11B2 expression. Whole-cell recordings in HAC15 cells indicated robust endogenous ATP2B4 conductance in native cells but reduced conductance with overexpressed WT and variant ATP2B4. The previously defined PA-causing ATP2B3 variant served as a positive control and exhibited elevated CYP11B2 mRNA. In conclusion, while this study did not confirm a pathogenic role for ATP2B4 variants in BHA, we describe the sequencing analysis for familial and sporadic BHA and outline a template for the thorough in vitro characterization of gene variants.
原醛症(PA)是继发性高血压最常见的病因,在难治性高血压患者中发病率较高。尽管最近在醛固酮产生腺瘤(APA)相关 PA 中发现了体细胞变异,但双侧醛固酮产生(双侧醛固酮增多症;BHA)引起的 PA 原因仍不清楚。在此,我们在 BHA 患者队列中鉴定了罕见的 ATP2B4 基因突变。ATP2B4 属于与 APA 发病机制相关的 ATP2B3 钙-ATP 酶家族。研究了肾上腺组织中内源性 ATP2B4 的表达,并对基因变异进行了功能分析,以研究其对醛固酮合酶(CYP11B2)表达、基础和激动剂刺激条件下类固醇生成的影响,以及对通道特性的生物物理特性的改变。在 HAC15 中敲低 ATP2B4,其中一个 shRNA 克隆中对血管紧张素 II 的刺激减少。生成了具有四环素(dox)诱导的野生型和变异型 ATP2B4 的稳定 HAC15 细胞系,并证实 dox 诱导的 ATP2B4 mRNA 和蛋白上调。然而,ATP2B4 变体并未改变基础或激动剂刺激的 CYP11B2 表达。HAC15 细胞的全细胞记录表明,在天然细胞中存在强大的内源性 ATP2B4 电导,但与过表达的 WT 和变体 ATP2B4 相比,电导降低。先前定义的引起 PA 的 ATP2B3 变体作为阳性对照,表现出 CYP11B2 mRNA 的升高。总之,虽然本研究并未证实 ATP2B4 变体在 BHA 中的致病性作用,但我们描述了家族性和散发性 BHA 的测序分析,并概述了基因变异的全面体外特征描述模板。