Centro Alta Tecnologia "Istituto di Ricerche Chimiche e Biochimiche G. Ronzoni" Srl, via G. Colombo 81, 20133 Milan, Italy.
Department of Biological Engineering, Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, 77 Massachusetts Avenue, Cambridge MA, 02139, United States.
Carbohydr Polym. 2020 Apr 15;234:115913. doi: 10.1016/j.carbpol.2020.115913. Epub 2020 Jan 27.
Rapid advances have been made in developing analytical technologies for characterization of highly heterogeneous active ingredients of complex drugs, such as pentosan polysulfate (PPS), active ingredient of the drug Elmiron®, approved by the Food and Drug Administration and marketed in the United States to treat interstitial cystitis. PPS sulfated polysaccharides comprise of a repeat unit of β(1-4)-D-xylopyranoses randomly substituted by 4-O-methyl-glucopyranosyluronic acid. To define the critical quality attributes (CQAs) of such a complex drug, it is critical to develop an approach that integrates data from orthogonal analytical methodologies. Here, we developed an approach integrating diverse analytical tools including gel permeation chromatography, LC/ESI-MS and NMR to measure CQAs of PPS. The proposed mathematical framework integrates the data from these diverse analytical methods as function of PPS chain length and building blocks. Our approach would facilitate in establishing a scientific foundation for comparative characterization of drug products with complex active ingredients.
在开发分析技术以表征复杂药物(如戊聚糖多硫酸酯(PPS),Elmiron®药物的活性成分,已获美国食品和药物管理局批准并在美国上市,用于治疗间质性膀胱炎)的高度不均匀活性成分方面取得了快速进展。PPS 硫酸化多糖由β(1-4)-D-木吡喃糖的重复单元组成,随机取代 4-O-甲基-吡喃葡萄糖醛酸。为了定义此类复杂药物的关键质量属性(CQAs),开发一种整合来自正交分析方法的数据的方法至关重要。在这里,我们开发了一种整合多种分析工具的方法,包括凝胶渗透色谱、LC/ESI-MS 和 NMR,以测量 PPS 的 CQAs。所提出的数学框架将这些不同分析方法的数据整合为 PPS 链长和构建块的函数。我们的方法将有助于为具有复杂活性成分的药物产品的比较特性建立科学基础。