Department of Pathology and Laboratory Medicine, Weill Cornell Medicine, 1300 York Avenue, New York, NY, 10065, USA.
Caryl and Israel Englander Institute for Precision Medicine, Weill Cornell Medicine and NewYork-Presbyterian, 413 East 69th Street, New York, NY, 10021, USA.
Acta Neuropathol Commun. 2020 Jun 3;8(1):80. doi: 10.1186/s40478-020-00951-4.
BCOR has been recognized as a recurrently altered gene in a subset of pediatric tumors of the central nervous system (CNS). Here, we describe a novel BCOR-CREBBP fusion event in a case of pediatric infiltrating astrocytoma and further probe the frequency of related fusion events in CNS tumors. We analyzed biopsy samples taken from a 15-year-old male with an aggressive, unresectable and multifocal infiltrating astrocytoma. We performed RNA sequencing (RNA-seq) and targeted DNA sequencing. In the index case, the fused BCOR-CREBBP transcript comprises exons 1-4 of BCOR and exon 31 of CREBBP. The fused gene thus retains the Bcl6 interaction domain of BCOR while eliminating the domain that has been shown to interact with the polycomb group protein PCGF1. The fusion event was validated by FISH and reverse transcriptase PCR. An additional set of 177 pediatric and adult primary CNS tumors were assessed via FISH for BCOR break apart events, all of which were negative. An additional 509 adult lower grade infiltrating gliomas from the publicly available TCGA dataset were screened for BCOR or CREBBP fusions. In this set, one case was found to harbor a CREBBP-GOLGA6L2 fusion and one case a CREBBP-SRRM2 fusion. In a third patient, both BCOR-L3MBTL2 and EP300-BCOR fusions were seen. Of particular interest to this study, EP300 is a paralog of CREBBP and the breakpoint seen involves a similar region of the gene to that of the index case; however, the resultant transcript is predicted to be completely distinct. While this gene fusion may play an oncogenic role through the loss of tumor suppressor functions of BCOR and CREBBP, further screening over larger cohorts and functional validation is needed to determine the degree to which this or similar fusions are recurrent and to elucidate their oncogenic potential.
BCOR 已被确认为中枢神经系统 (CNS) 儿童肿瘤亚群中反复改变的基因。在这里,我们描述了一例儿童浸润性星形细胞瘤中新型的 BCOR-CREBBP 融合事件,并进一步探讨了 CNS 肿瘤中相关融合事件的频率。我们分析了一名 15 岁男性侵袭性、不可切除和多灶性浸润性星形细胞瘤的活检样本。我们进行了 RNA 测序 (RNA-seq) 和靶向 DNA 测序。在索引病例中,融合的 BCOR-CREBBP 转录本包含 BCOR 的外显子 1-4 和 CREBBP 的外显子 31。融合基因因此保留了 BCOR 的 Bcl6 相互作用结构域,同时消除了已显示与多梳蛋白组蛋白 PCGF1 相互作用的结构域。融合事件通过 FISH 和逆转录 PCR 进行了验证。通过 FISH 评估了另外一组 177 例儿童和成人原发性 CNS 肿瘤的 BCOR 分离事件,所有这些事件均为阴性。在可公开获得的 TCGA 数据集筛选了另外 509 例成人低级别浸润性神经胶质瘤,以筛查 BCOR 或 CREBBP 融合。在这组中,有 1 例存在 CREBBP-GOLGA6L2 融合,1 例存在 CREBBP-SRRM2 融合。在第 3 例患者中,发现了 BCOR-L3MBTL2 和 EP300-BCOR 融合。本研究特别感兴趣的是,EP300 是 CREBBP 的同源基因,所涉及的基因断点与索引病例相似;然而,预测产生的转录本是完全不同的。虽然这种基因融合可能通过失去 BCOR 和 CREBBP 的肿瘤抑制功能发挥致癌作用,但需要进一步在更大的队列中进行筛选和功能验证,以确定这种或类似融合的反复出现程度,并阐明其致癌潜力。