X连锁重症联合免疫缺陷的基因治疗：历史成果与现状 - Suppr

Gene therapy for X-linked severe combined immunodeficiency: Historical outcomes and current status.

作者信息

Pai Sung-Yun, Thrasher Adrian J

机构信息

Division of Hematology-Oncology, Boston Children's Hospital and Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Mass.

University College London Great Ormond Street Institute of Child Health, and Great Ormond Street Hospital for Children NHS Foundation Trust, London, United Kingdom.

出版信息

J Allergy Clin Immunol. 2020 Aug;146(2):258-261. doi: 10.1016/j.jaci.2020.05.055. Epub 2020 Jun 16.

DOI:10.1016/j.jaci.2020.05.055

PMID:32561390

Abstract

摘要

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Gene therapy for X-linked severe combined immunodeficiency: Historical outcomes and current status.

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