In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation.
作者信息
Moreno Ana M, Fu Xin, Zhu Jie, Katrekar Dhruva, Shih Yu-Ru V, Marlett John, Cabotaje Jessica, Tat Jasmine, Naughton John, Lisowski Leszek, Varghese Shyni, Zhang Kang, Mali Prashant
出版信息
Mol Ther. 2020 Aug 5;28(8):1931. doi: 10.1016/j.ymthe.2020.06.027. Epub 2020 Jun 29.
Abstract
摘要
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