Department of Haematology, The Royal Marsden Hospital, London, UK.
Division of Molecular Pathology, The Institute of Cancer Research (ICR) and The Royal Marsden Hospital, 123 Old Brompton Road, London, SW7 3RP, UK.
Ann Hematol. 2020 Aug;99(8):1793-1804. doi: 10.1007/s00277-020-04149-5. Epub 2020 Jul 1.
The phase 3, double-blind, placebo-controlled TOURMALINE-MM3 study (NCT02181413) demonstrated improved progression-free survival with ixazomib maintenance versus placebo post autologous stem cell transplant (ASCT) in multiple myeloma patients. We report additional safety data from TOURMALINE-MM3 to inform adverse event (AE) management recommendations. Patients were randomized 3:2 to receive ixazomib (n = 395) or placebo (n = 261) on days 1, 8, and 15 of 28-day cycles for ~ 2 years or until progressive disease/toxicity. The initial 3-mg ixazomib dose was escalated to 4 mg in cycle 5, if tolerated in cycles 1-4. Safety was a secondary endpoint assessed in all treated patients; AEs were graded using Common Terminology Criteria for AEs v4.03. The rate of grade ≥ 3 AEs was higher in the ixazomib arm (19%) than in the placebo arm (5%), but the rate of discontinuation due to AEs was similar (7% vs. 5%). For AEs of clinical interest, rates were higher with ixazomib versus placebo: nausea 39% versus 15%, vomiting 27% versus 11%, diarrhea 35% versus 24%, thrombocytopenia 13% versus 3%, and peripheral neuropathy 19% versus 15%. However, the majority of events were low-grade, manageable with supportive therapy or dose reduction, and reversible, and did not result in discontinuation. There was no evidence of cumulative, long-term, or late-onset toxicity with ixazomib maintenance. Ixazomib is an efficacious and tolerable option for post-ASCT maintenance. AEs associated with ixazomib maintenance can be managed in the context of routine post-ASCT supportive care due to the limited additional toxicity. ClinicalTrials.gov NCT02181413.
TOURMALINE-MM3 是一项 3 期、双盲、安慰剂对照研究(NCT02181413),结果显示,在多发性骨髓瘤患者自体干细胞移植(ASCT)后,与安慰剂相比,伊沙佐米维持治疗可改善无进展生存期。我们报告了 TOURMALINE-MM3 的额外安全性数据,以提供不良事件(AE)管理建议。患者按 3:2 的比例随机分配至伊沙佐米(n = 395)或安慰剂(n = 261)组,接受为期 2 年或直至疾病进展/毒性的 28 天周期治疗,在每个周期的第 1、8 和 15 天用药,初始剂量为 3 毫克伊沙佐米,在第 1-4 周期耐受时可升至 4 毫克。所有治疗患者均评估安全性,采用通用不良事件术语标准 4.03 对 AE 进行分级。伊沙佐米组(19%)的≥3 级 AE 发生率高于安慰剂组(5%),但因 AE 停药率相似(7% vs. 5%)。对于具有临床意义的 AE,伊沙佐米组发生率高于安慰剂组:恶心 39% vs. 15%,呕吐 27% vs. 11%,腹泻 35% vs. 24%,血小板减少症 13% vs. 3%,周围神经病 19% vs. 15%。但是,大多数事件为低级别,可通过支持性治疗或剂量减少进行管理,且可逆转,不会导致停药。伊沙佐米维持治疗无累积、长期或迟发性毒性的证据。伊沙佐米是 ASCT 后维持治疗的一种有效且可耐受的选择。由于额外毒性有限,与伊沙佐米维持治疗相关的 AE 可在 ASCT 后常规支持性治疗背景下进行管理。ClinicalTrials.gov NCT02181413。