Department of Human Genetics, Leiden University Medical Center, Leiden, Netherlands.
CHU de Québec Research Centre (site CHUL) and Laboratory for Skin Cancer Research and Axe Neuroscience, Université Laval, Québec, Canada.
J Exp Med. 2020 Nov 2;217(11). doi: 10.1084/jem.20191688.
The autosomal recessive immunodeficiency, centromeric instability, and facial anomalies (ICF) syndrome is a genetically heterogeneous disorder. Despite the identification of the underlying gene defects, it is unclear how mutations in any of the four known ICF genes cause a primary immunodeficiency. Here we demonstrate that loss of ZBTB24 in B cells from mice and ICF2 patients affects nonhomologous end-joining (NHEJ) during immunoglobulin class-switch recombination and consequently impairs immunoglobulin production and isotype balance. Mechanistically, we found that ZBTB24 associates with poly(ADP-ribose) polymerase 1 (PARP1) and stimulates its auto-poly(ADP-ribosyl)ation. The zinc-finger in ZBTB24 binds PARP1-associated poly(ADP-ribose) chains and mediates the PARP1-dependent recruitment of ZBTB24 to DNA breaks. Moreover, through its association with poly(ADP-ribose) chains, ZBTB24 protects them from degradation by poly(ADP-ribose) glycohydrolase (PARG). This facilitates the poly(ADP-ribose)-dependent assembly of the LIG4/XRCC4 complex at DNA breaks, thereby promoting error-free NHEJ. Thus, we uncover ZBTB24 as a regulator of PARP1-dependent NHEJ and class-switch recombination, providing a molecular basis for the immunodeficiency in ICF2 syndrome.
常染色体隐性免疫缺陷、着丝粒不稳定和面部异常(ICF)综合征是一种遗传异质性疾病。尽管已经确定了潜在的基因缺陷,但尚不清楚四个已知的 ICF 基因中的任何突变如何导致原发性免疫缺陷。在这里,我们证明了小鼠和 ICF2 患者 B 细胞中 ZBTB24 的缺失会影响免疫球蛋白类别转换重组过程中的非同源末端连接(NHEJ),从而损害免疫球蛋白的产生和同种型平衡。从机制上讲,我们发现 ZBTB24 与聚(ADP-核糖)聚合酶 1(PARP1)结合并刺激其自身聚(ADP-核糖)化。ZBTB24 中的锌指结合 PARP1 相关的聚(ADP-核糖)链,并介导 ZBTB24 依赖 PARP1 募集到 DNA 断裂处。此外,通过与聚(ADP-核糖)链的结合,ZBTB24 防止它们被聚(ADP-核糖)糖水解酶(PARG)降解。这促进了 LIG4/XRCC4 复合物在 DNA 断裂处的无错误 NHEJ 组装,从而促进了无错误的 NHEJ。因此,我们揭示了 ZBTB24 作为 PARP1 依赖性 NHEJ 和类别转换重组的调节剂,为 ICF2 综合征的免疫缺陷提供了分子基础。