Grabowski Gregory A, Antommaria Armand H M, Kolodny Edwin H, Mistry Pramod K
Department of Pediatrics, University of Cincinnati College of Medicine, United States of America; Department of Molecular Genetics, Biochemistry and Microbiology, University of Cincinnati College of Medicine, United States of America; Division of Human Genetics, Cincinnati Children's Research Foundation, Cincinnati, OH, United States of America.
Department of Pediatrics, University of Cincinnati College of Medicine, United States of America; Lee Ault Carter Chair of Pediatric Ethics, Cincinnati Children's Research Foundation, Cincinnati, OH, United States of America.
Mol Genet Metab. 2021 Feb;132(2):59-75. doi: 10.1016/j.ymgme.2020.12.291. Epub 2020 Dec 29.