Infantile spinal muscular atrophy - the potential for cure of a fatal disease.
作者信息
Volpe J J
机构信息
Department of Neurology, Harvard Medical School, Boston, MA, USA.
Department of Pediatric Newborn Medicine, Harvard Medical School, Boston, MA, USA.
出版信息
J Neonatal Perinatal Med. 2021;14(2):153-157. doi: 10.3233/NPM-200680.
Abstract
摘要
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