Magee-Womens Research Institute, 204 Craft Avenue, Room B509, Pittsburgh, Pennsylvania, 15213, USA.
James Graham Brown Cancer Center, University of Louisville School of Medicine, Louisville, Kentucky, USA.
AAPS PharmSciTech. 2021 Feb 24;22(3):83. doi: 10.1208/s12249-021-01931-0.
Griffithsin (GRFT) has shown potent anti-HIV activity, and it is being developed as a drug candidate for HIV prevention. Successful implementation requires thorough understanding of its preformulation characterization. In this work, preformulation assessments were conducted to characterize GRFT and identify its degradation pathways under selected conditions of temperature, light, pH, shear, ionic strength, and oxidation. Compatibility with vaginal fluid simulant, vaginal enzymes, Lactobacillus spp., and human cervicovaginal secretions was assessed. The purity, melting temperature, and HIV gp120-binding affinity of GRFT stored at 4°C and 25°C in phosphate-buffered saline (PBS) were assessed for 2 years. Chemical modifications were evaluated by intact mass analysis and peptide sequencing. Excised human ectocervical tissue permeability and localization of GRFT were evaluated. Our results demonstrated GRFT to be safe and stable under all the preformulation assessment conditions studied except oxidative stress. When GRFT was exposed to hydrogen peroxide or human cervicovaginal secretion, methionine 78 in the protein sequence underwent oxidation. GRFT did not permeate through human cervical tissue but adhered to the superficial epithelial tissue. The 2-year stability study revealed no significant change in GRFT's aggregation, degradation, melting temperature, or gp120-binding affinity despite a slow increase in oxidation over time. These studies elucidated desirable safety and bioactivity profile for GRFT, showing promise as a potential drug candidate for HIV prevention. However, susceptibility to oxidative degradation was identified. Effective protection of GRFT from oxidation is required for further development.
格夫司亭(GRFT)具有很强的抗 HIV 活性,目前正在被开发为一种 HIV 预防候选药物。成功实施需要彻底了解其预配方特征。在这项工作中,进行了预配方评估,以表征 GRFT 并确定其在选定的温度、光照、pH 值、剪切力、离子强度和氧化条件下的降解途径。还评估了与阴道液模拟物、阴道酶、乳杆菌属和人宫颈阴道分泌物的相容性。评估了在磷酸盐缓冲盐水(PBS)中于 4°C 和 25°C 储存 2 年的 GRFT 的纯度、熔点和 HIV gp120 结合亲和力。通过完整质量分析和肽测序评估化学修饰。评估了 GRFT 的人宫颈外植体组织渗透性和定位。我们的研究结果表明,GRFT 在除氧化应激以外的所有预配方评估条件下都是安全且稳定的。当 GRFT 暴露于过氧化氢或人宫颈阴道分泌物时,蛋白质序列中的蛋氨酸 78 发生氧化。GRFT 不会透过人宫颈组织,但会附着在表面上皮组织上。2 年的稳定性研究表明,尽管随着时间的推移氧化缓慢增加,但 GRFT 的聚集、降解、熔点或 gp120 结合亲和力没有明显变化。这些研究阐明了 GRFT 的理想安全性和生物活性特征,显示出作为 HIV 预防候选药物的潜力。然而,GRFT 易发生氧化降解。需要有效保护 GRFT 免受氧化,以进一步开发。