McKusick-Nathans Department of Genetic Medicine, Johns Hopkins University School of Medicine, 733 N. Broadway, 470 Miller Research Building, Baltimore, MD 21205, USA.
Department of Developmental and Cell Biology, University of California, Irvine, Natural Sciences II, CA 92697, USA.
Hum Mol Genet. 2021 Apr 30;30(6):485-499. doi: 10.1093/hmg/ddab064.
Pancreatic ductal adenocarcinoma (PDAC) is an aggressive form of cancer with high mortality. The cellular origins of PDAC are largely unknown; however, ductal cells, especially centroacinar cells (CACs), have several characteristics in common with PDAC, such as expression of SOX9 and components of the Notch-signaling pathway. Mutations in KRAS and alterations to Notch signaling are common in PDAC, and both these pathways regulate the transcription factor SOX9. To identify genes regulated by SOX9, we performed siRNA knockdown of SOX9 followed by RNA-seq in PANC-1s, a human PDAC cell line. We report 93 differentially expressed (DE) genes, with convergence on alterations to Notch-signaling pathways and ciliogenesis. These results point to SOX9 and Notch activity being in a positive feedback loop and SOX9 regulating cilia production in PDAC. We additionally performed ChIP-seq in PANC-1s to identify direct targets of SOX9 binding and integrated these results with our DE gene list. Nine of the top 10 downregulated genes have evidence of direct SOX9 binding at their promoter regions. One of these targets was the cancer stem cell marker EpCAM. Using whole-mount in situ hybridization to detect epcam transcript in zebrafish larvae, we demonstrated that epcam is a CAC marker and that Sox9 regulation of epcam expression is conserved in zebrafish. Additionally, we generated an epcam null mutant and observed pronounced defects in ciliogenesis during development. Our results provide a link between SOX9, EpCAM and ciliary repression that can be exploited in improving our understanding of the cellular origins and mechanisms of PDAC.
胰腺导管腺癌(PDAC)是一种具有高死亡率的侵袭性癌症。PDAC 的细胞起源在很大程度上是未知的;然而,导管细胞,特别是中心腺泡细胞(CAC),与 PDAC 有几个共同特征,例如 SOX9 的表达和 Notch 信号通路的成分。KRAS 突变和 Notch 信号通路改变在 PDAC 中很常见,这两种途径都调节转录因子 SOX9。为了鉴定受 SOX9 调控的基因,我们在人 PDAC 细胞系 PANC-1s 中进行了 SOX9 的 siRNA 敲低,然后进行 RNA-seq。我们报告了 93 个差异表达(DE)基因,其特征在于 Notch 信号通路和纤毛发生的改变。这些结果表明 SOX9 和 Notch 活性处于正反馈回路中,SOX9 调节 PDAC 中的纤毛生成。我们还在 PANC-1s 中进行了 ChIP-seq,以鉴定 SOX9 结合的直接靶基因,并将这些结果与我们的 DE 基因列表整合。前 10 个下调基因中有 9 个证据表明其启动子区域有直接的 SOX9 结合。其中一个靶标是癌症干细胞标记物 EpCAM。通过在斑马鱼幼虫中进行全胚胎原位杂交以检测 epcam 转录物,我们证明了 epcam 是 CAC 标记物,并且 Sox9 对 epcam 表达的调节在斑马鱼中是保守的。此外,我们生成了一个 epcam 缺失突变体,并观察到在发育过程中纤毛发生明显缺陷。我们的结果提供了 SOX9、EpCAM 和纤毛抑制之间的联系,这可以被利用来提高我们对 PDAC 的细胞起源和机制的理解。