Monash Children's Hospital, Melbourne, Australia.
Monash University, Melbourne, Australia.
J Child Neurol. 2021 Oct;36(11):935-942. doi: 10.1177/08830738211009654. Epub 2021 May 31.
CLIPPERS (chronic lymphocytic inflammation with pontine perivascular enhancement responsive to steroids) is an extremely rare neurologic inflammatory condition. Fewer than 10 pediatric cases have been described.Debate persists as to whether it is a distinct disease or a clinical, radiologic, and histologic phenotype evolving into another disorder. We propose that CLIPPERS may be a clinical manifestation of an underlying state of immune-dysregulation.We describe the case of the youngest known report of CLIPPERS, an 18-month-old infant from Melbourne, Australia. Reviewing the literature for all reported pediatric cases, we identified that robust investigation and whole exome sequencing was underutilized and proposed diagnostic criteria were frequently unmet. Particular focus should be paid to genes known to cause familial hemophagocytic lymphohistiocytosis (HLH), with the CLIPPERS phenotype manifesting as a form of isolated central nervous system (CNS)-HLH in some patients. Curative treatment options such as hematopoietic stem cell transplantation may be appropriate for some patients and should be considered early.
CLIPPERS(慢性淋巴细胞性炎症伴桥脑血管周围强化对类固醇有反应)是一种极其罕见的神经系统炎症性疾病。仅有不到 10 例儿科病例被描述。关于它是否是一种独特的疾病,还是一种发展为另一种疾病的临床、放射学和组织学表型,仍存在争议。我们提出 CLIPPERS 可能是免疫失调潜在状态的临床表现。我们描述了来自澳大利亚墨尔本的已知最年轻的 CLIPPERS 病例,这是一名 18 个月大的婴儿。我们对所有报告的儿科病例进行文献回顾,发现对其进行全面检查和外显子组测序的应用不足,且经常未满足诊断标准。应特别注意已知可引起家族性噬血细胞性淋巴组织细胞增生症(HLH)的基因,一些患者的 CLIPPERS 表型表现为一种孤立性中枢神经系统(CNS)-HLH。造血干细胞移植等治愈性治疗选择可能对一些患者合适,应尽早考虑。