Abidi Asima, Gorris Mark A J, Brennan Evan, Jongmans Marjolijn C J, Weijers Dilys D, Kuiper Roland P, de Voer Richarda M, Hoogerbrugge Nicoline, Schreibelt Gerty, de Vries I Jolanda M
Department of Tumor Immunology, Radboud Institute for Molecular Life Sciences, Radboud University Medical Center, 6525 GA Nijmegen, The Netherlands.
Princess Máxima Center for Pediatric Oncology, 3584 CS Utrecht, The Netherlands.
Cancers (Basel). 2021 May 13;13(10):2345. doi: 10.3390/cancers13102345.
Lynch syndrome (LS) and constitutional mismatch repair deficiency (CMMRD) are hereditary disorders characterised by a highly increased risk of cancer development. This is due to germline aberrations in the mismatch repair (MMR) genes, which results in a high mutational load in tumours of these patients, including insertions and deletions in genes bearing microsatellites. This generates microsatellite instability and cause reading frameshifts in coding regions that could lead to the generation of neoantigens and opens up avenues for neoantigen targeting immune therapies prophylactically and therapeutically. However, major obstacles need to be overcome, such as the heterogeneity in tumour formation within and between LS and CMMRD patients, which results in considerable variability in the genes targeted by mutations, hence challenging the choice of suitable neoantigens. The machine-learning methods such as NetMHC and MHCflurry that predict neoantigen- human leukocyte antigen (HLA) binding affinity provide little information on other aspects of neoantigen presentation. Immune escape mechanisms that allow MMR-deficient cells to evade surveillance combined with the resistance to immune checkpoint therapy make the neoantigen targeting regimen challenging. Studies to delineate shared neoantigen profiles across patient cohorts, precise HLA binding algorithms, additional therapies to counter immune evasion and evaluation of biomarkers that predict the response of these patients to immune checkpoint therapy are warranted.
林奇综合征(LS)和遗传性错配修复缺陷(CMMRD)是遗传性疾病,其特征是癌症发生风险显著增加。这是由于错配修复(MMR)基因的种系畸变,导致这些患者肿瘤中的高突变负荷,包括携带微卫星的基因中的插入和缺失。这会产生微卫星不稳定性,并在编码区域导致阅读框移位,从而可能导致新抗原的产生,并为预防性和治疗性的新抗原靶向免疫疗法开辟了途径。然而,需要克服一些主要障碍,例如LS和CMMRD患者内部和之间肿瘤形成的异质性,这导致突变靶向基因存在相当大的变异性,从而对合适新抗原的选择构成挑战。诸如NetMHC和MHCflurry等预测新抗原与人类白细胞抗原(HLA)结合亲和力的机器学习方法,在新抗原呈递的其他方面提供的信息很少。允许错配修复缺陷细胞逃避免疫监视的免疫逃逸机制,加上对免疫检查点疗法的抗性,使得新抗原靶向方案具有挑战性。有必要开展研究,以描绘不同患者群体的共享新抗原谱、精确的HLA结合算法、对抗免疫逃逸的其他疗法,以及评估预测这些患者对免疫检查点疗法反应的生物标志物。